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- Adeno-associated virus serotype 5 containing the human RDH12 gene
- Adeno-associated virus serotype 8 containing the human RdCVF sequence and the human RdCVFL sequence
- Combination of three adeno-associated viral vectors of serotype 8 containing the 5'-, the body- and the 3'- coding sequences of human CEP290 fused to inteins
- Mixture of two adeno-associated viral vectors serotype 8 containing the 5'-half sequence of human MYO7A gene and the 3'-half sequence of human MYO7A gene