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22 Result(s)
Substance(s)
- (2S)-2-{[(2R)-2-[({[3,3-dibutyl-7-(methylthio)-1,1-dioxido-5-phenyl-2,3,4,5-tetrahydro-1,2,5-benzothiadiazepin-8-yl]oxy}acetyl)amino]-2-(4-hydroxyphenyl)acetyl]amino}butanoic acid
- (S)-3'-(OH)-desazadesferrithiocin-polyether, magnesium salt
- Adeno -associated viral vector serotype 8 containing the human functional version of UGT1A1 gene
- Adeno-associated viral vector containing porphobilinogen deaminase gene
- Adeno-associated viral vector serotype 3B encoding human multidrug resistance protein 3A
- Afamelanotide
- Bitopertin
- Ciclopirox
- Dersimelagon
- Givosiran
- Hemin
- Heterologous human adult liver derived stem cells
- Maralixibat chloride
- Modified mRNA encoding the UGT1A1 protein
- Recombinant human porphobilinogen deaminase
- Titanium dioxide and bisoctrizole
- Volrubigene ralaparvovec