Search for an orphan drug
51 Result(s)
- (-)-trans-3-(5,6-dihydro-4H-pyrrolo[3,2,1-ij]quinolin-1yl)-4-(1H-indol-3-yl) pyrrolidine-2, 5-dione
- (1-methyl-2-nitro-1H-imidazole-5-yl)methyl N,N'-bis(2-bromoethyl) diamidophosphate
- 16-base single-stranded peptide nucleic acid oligonucleotide linked to a 7-amino acid peptide
- 18-(p-(131I)-iodophenyl)octadecyl phosphocholine
- 3-(5-cyano-4-(cyclopropylamino)pyridin-2-yl)-1-(6-formyl-5-((4-methyl-2-oxopiperazin-1-yl)methyl)pyridin-2-yl)-1-methylurea
- 4-oxo-4H-chromene-2-carboxylic acid (2-(2-4-(2-(6,7-dimethoxy-3,4-dihydro-1H-isoquinolin-2-yl)-ethyl)-phenyl-2H-tetrazol-5-yl)-4,5-dimethoxy-phenyl)-amide
- 7-ethyl-10-hydroxy-camptothecin
- Anlotinib
- Autologous CD4+ and CD8+ T cells transduced with a lentiviral vector encoding an affinity enhanced T cell receptor specific to MAGE-A4
- Autologous CD4+ and CD8+ T cells transduced with lentiviral vector containing an affinity-enhanced T-cell receptor targeting the New York esophageal antigen-1
- Brostallicin
- Camsirubicin
- Cis-diamminedichloroplatinum(II) (CDDP), vinblastine sulfate, 8-((2-hydroxybenzoyl)amino)octanoate (SHAO-FA)
- Crenolanib besylate
- Deforolimus
- Doxorubicin
- Doxorubicin hydrochloride (liposomal)
- Doxorubicin(6-maleimidocaproyl)hydrazone
- Fenretinide
- Genetically modified serotype 5/3 adenovirus coding for granulocyte-macrophage colony-stimulating factor
- Human/murine chimeric monoclonal antibody against endoglin
- Humanized IgG1anti-AXL-antibody conjugated to monomethyl auristatin E
- Humanized immunoglobulin IgG1k-agonistic monoclonal antibody that binds to CD40
- Idronoxil
- Imatinib mesilate
- Larotrectinib
- Mammalian target of rapamcyin (mTOR) inhibitor
- N-acetylsarcosyl-glycyl-L-valyl-D-allo-isoleucyl-L-threonyl-L-norvalyl-L-isoleucyl-L-arginyl-L-prolyl-N-ethylamide
- Nirogacestat
- Olaratumab
- Ombrabulin
- Onfekafusp alfa
- Paclitaxel
- Palifosfamide
- Propranolol hydrochloride
- Sindbis virus envelope pseudotyped lentiviral vector encoding New York oesophageal squamous cell carcinoma-1 protein
- Single Protein Encapsulated Doxorubicin
- Small molecule composed of a ligand binding moiety to BRD9, a chemical linker, and a ligand binding moiety to the cereblon (CRBN) E3 ligase
- Spiro[3H-Indole-3,2-pyrrolidin]-2(1H)-one derivative
- Trabectedin
- Unesbulin
- Vinorelbine tartrate
- Yttrium (90Y)-DTPA-radiolabelled chimeric monoclonal antibody against frizzled homologue 10