Búsqueda de un medicamento huérfano
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66 Resultado(s)
- (1E,6E)-1,7-bis(3,4-dimethoxyphenyl)-4-cyclobutylmethyl-1,6-heptadiene-3,5-dione
- (6R)-4, 5, 6, 7-tetrahydro-N6-propyl-2, 6-benzothiazolediamine dihydrochloride monohydrate
- (R)-troloxamide quinone
- 1-[(2-Chloro-4-methoxyphenoxy)methyl]-4-[(2,6-dichlorophenoxy)methyl]benzene
- 6-etinil-1-(pentano-3-il)-1H-imidazo[4,5-b]pirazin-2(3H)-ona
- Lactobacillus plantarum
- Adeno-associated viral vector serotype 9 containing the human SMN gene
- Adeno-associated viral vector serotype hu68 containing the human SMN1 gene
- Adeno-associated virus serotype 9 expressing the human Survival Motor Neuron gene
- Ambroxol hydrochloride
- Anticuerpo monoclonal recombinante humanizado de clase IgG1/kappa contra la proteína humana Nogo-A
- Arimoclomol
- Autologous Olfactory Neural Progenitors
- Autologous adipose derived mesenchymal stromal cells
- Brivaracetam
- Celecoxib , Ciprofloxacin
- Clorito de sodio
- Colest-4-en-3-ona, oxima
- Células mesenquimales de estroma derivadas de médula ósea autóloga secretoras de factores neurotróficos
- Células progenitoras de neuronas motoras alogénicas procedentes de células madre embrionarias humanas
- DNA plasmid vector (pCK-HGFX7) expressing human hepatocyte growth factor
- Diclorhidrato de 5-[1-(2,6-diclorobencil)piperidina-4-ilmetoxi]quinazolina-2,4-diamina
- Edaravone
- Enoxacin
- Factor de crecimiento endotelial vascular recombinante humano
- Fenilbutirato de sodio
- Filgrastim
- Gliceril tri-(4-fenilbutirato)
- H-Leu-Pro-Pro-Leu-Pro-Tyr-Pro-OH
- Human anti-promyostatin monoclonal antibody
- Human culture expanded autologous mesenchymal stromal cells
- Hydrocinnamate-[Orn-Pro-dCha-Trp-Arg]acetate
- Ibudilast
- L-pyroglutamyl-L-asparaginyl-L-prolyl-D-tyrosyl-D-tryptophan amide
- LMI 070
- Late Stage Human Motor Neutron Progenitors
- Levosimendan
- Mesilato de masitinib
- Oligonucleótido antisentido dirigido contra el gen SMN2
- Oligopeptide containing 6 amino acids (H-Phe-Ser-Arg-Tyr-Ala-Arg-OH)
- Recombinant human antibody directed against misfolded human superoxide dismutase 1
- Recombinant human cerebral dopamine neurotrophic factor (CDNF)
- Reldesemtiv
- Riluzol
- Risdiplam
- Sarsapogenin
- Smilagenina
- Sodium phenylbutyrate, tauroursodeoxycholic acid
- Sulfato de dextrano de bajo peso molecular
- Synthetic ribonucleic acid oligonucleotide directed against superoxide dismutase 1 (SOD-1) messenger ribonucleic acid
- Talampanel
- Tauroursodeoxycholic acid (TUDCA)
- Valproato sodico
- Vector vírico que contiene ADN que codifica la proteína humana SMN
- Xaliproden hydrochloride
- [S]+ apomorfina
- adeno-associated viral vector serotype 9 encoding miRNA against human superoxide dismutase 1
- caprine hyperimmune serum against HIV lysate