Orphanet: Búsqueda de un medicamento huérfano
Búsqueda de un medicamento huérfano
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87 Resultado(s)
(5R,5aR,8aR,9S)-9-[[4,6-O-[(R)-etilideno]-beta-D-glucopiranosil]-oxi]-5-(4-({[(2,2-dimetil-1,3-dioxolan-4-il)metoxi]carbonil}oxi)-3,5-dimetoxifenil)-5,8,8a,9-tetrahidroisobenzofuro[5,6-f][1,3]benzodioxol-6(5aH)-on
(R) -6-(2-fluorophenyl) -N-(3-(2-((2 -methoxyethyl)amino)ethyl)phenyl)-5,6 - dihydrobenzo[h]quinazolin -2-amine dihydrochlorid
1-((2S,4S)-2-((((S)-(4-bromophenoxy)(((S)-1-oxo-1-(((S)-pentan-2-yl)oxy)propan-2-yl)amino)phosphoryl)oxy)methyl)-1,3-dioxolan-4-yl)-2-oxo-1,2-dihydropyrimidin-4-aminium chloride
1H-Benzimidazole-7-carboxamide, 2-[(2R)-2-methyl-2-pyrrolidinyl]
2-(2-phenylvinyl)-4-[4-methylpiperazin-1-yl)]-6-(5-methyl-2H-pyrazol-3-yl-amino)-pyrimidine L(+) tartrate salt
2-Chloro-N6-(3-iodobenzyl)adenosine-5'-N-methyluronamide
4-Amino-...-D-arabinofuranosyl]-...pyrimidinone
4-[2-(6-metilpiridina-2-il)-5,6-dihidro-4H-pirrolo [1,2-b] pirazol-3-il]-quinolina-6-carboxamida monohidrato
4-[3,5-bis(trimethylsilyl)benzamido] benzoic acid
5,10,15,20-tetrakis(2,6-difluoro-3-N-methylsulfamoylphenyl) bacteriochlorin
5-amino-1-(2-methyl-1H-benzo[d]imidazol-5-yl)-1H-pyrazol-4-yl 1H-indol-2-yl ketone mono[(S)-2-hydroxysuccinate]
6-thio-2'-deoxyguanosine
A genetically modified Salmonella comprising of methioninase
An autologous T-cell immunotherapy (ET140203)
Becatecarin
Bicistronic messenger ribonucleic acid (mRNA) encoding for ZF-DNMT and ZF-KRAB proteins, encapsulated in a lipid nanoparticle (LNP)
Bifunctional anti-PD-L1/TGFβ Trap fusion protein
Brivanib alaninato
Clorhidrato de (S)-10-[(dimetilamino)metil]-4-etil-9-hidroxi-4-O-[alpha-(2", 4", 5", 7"-tetranitro-9"-fluorenilidenoaminooxi)propionil]-1H-pirano[3', 4', 6', 7']indolizino[1,2-beta]-quinolina-3, 14-(4H, 12H)-diona
Devimistat
Diaspirin cross-linked haemoglobin
Doxorubicin carbon/iron magnetically targeted microparticles
Doxorubicin polyisohexylcyanoacrylate nanoparticles
Doxorubicina clorhidrato (en liposomas termosensibiles)
Ethiodized oil injection
Ezurpimtrostat
Fibroblast growth factor receptor (FGFR) inhibitor
Fimaporfin
Florilglutamic acid (18F)
Fosgemcitabine palabenamide
Futibatinib
IgG1 humanized antibody directed against Carcinoembryonic Antigen-related Cell Adhesion Molecule (CEACAM)1, 3 and 5
Infigratinib
Ivosidenib
Lenvatinib
Mefuparib
Mertansine functionalised gold nanoconjugate
Mifamurtide
N- 1',2-dihydroxy- 1,2'-binapthalen -4'-yl -4-methoxybenzenesulfonamide
N-(4-(4-amino-5-(3-fluoro-4-((4-methylpyrimidin-2-yl)oxy)phenyl)-7-methyl-7H-pyrrolo[2,3-d]pyrimidin-6-yl)phenyl)methacrylamide hydrochloride
N-(6-(2,6-dichloro-3,5-dimethoxyphenyl)-1H-pyrazolo[3,4-b]pyridin-3-yl)-4-(3,3-dimethylpiperazin-1-yl)benzamide hydrochloride
N-[4-(3-amino-1H-indazol-4 yl)phenyl]-N?-(2-fluoro-5-methylphenyl) urea
N-{2-[(6-{[(2,6-dichloro-3,5-dimethoxyphenyl)carbamoyl](methyl)amino}pyrimidin-4-yl)amino]-5-(4-ethylpiperazin-1-yl)phenyl}prop-2-enamide
NGR - factor de necrosis tumoral humano
Nanvuranlat
Nemorubicin hydrochloride
Nolatrexed
Oligosacárido monofosforilado sulfonatado de manosa
Pegylated arginine deiminase
Peretinoína
Porfimer sodium (for use with photodynamic therapy)
Ramucirumab
Recombinant human IL12/15-PDL1B HSV-1 oncolytic virus Injection
Recombinant oncolytic virus M1-c6v1
Rencofilstat
Resminostat
Seocalcitol
Silmitasertib
Sorafenib tosilato
Tegavivint
Thymalfasin
Tirapazamine
Tislelizumab
Tivantinib
Tremelimumab
Virus de la vacuna con timidina kinasa (TK) desactivada, que expresa GM-CSF
a humanized immunoglobulin IgG1 antibody with a kappa light chain (LC) which has high selectivity and specificity for cancer-specific plectin
an autologous T-cell immunotherapy (ECT204)
sodium 2-hydroxylinoleate
zanidatamab