Orphanet: Búsqueda de un medicamento huérfano
Búsqueda de un medicamento huérfano
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118 Resultado(s)
(3S)-(+)-(5-chloro-2-methoxifenil)-1,3-dihidro-3-flúor-6-(trifluoromethil)-2H-indol-2-uno
(S)-6-hidroxi-2,5,7,8-tetrametil-N-((R)-piperidin-3-il)croman-2-carboxamida hidrocloruro
2-[4-[[(2R)-2-ethoxy-3-[4-(trifluoromethyl)phenoxy]propyl]thio]-2-methylphenoxy]acetic acid (1:1) lysine dihydrate
3-Pentylbenzeneacetic acid sodium salt
4-bencil-2-naftalen-1-il-1,2,4-tiadiazolidin-3,5-diona
Acebutolol
Acetylleucine
Adeno-associated viral vector expressing human 21-hydroxylase
Adeno-associated viral vector expressing lipoprotein lipase
Alirocumab
Allogeneic cultured postnatal thymus-derived tissue
Alpha-tocopherol and ascorbic acid
Anticuerpo monoclonal IgG1 humano recombinante contra el factor de crecimiento de fibroblastos 23
Apolipoproteína A-I humana recombinante en un complejo fosfolipídico
Balipodect
Beloranib
Calcio acamprosato
Cannabidivarin
Carbetocina
Chenodeoxycholic acid
Cinacalcet
Crinecerfont
Células hematopoyéticas pluripotenciales autólogas transducidas con un vector lentivírico Lenti-D que contiene el cDNA del ABCD1 humano
Dantrolene sodium
Dasiglucagon
Dexamethasone sodium phosphate encapsulated in human erythrocytes
Diazoxide choline
Evolocumab
Exendin-(9-39)
Gemcabene
Glibenclamide
Glucagon analogue linked to a human immunoglobulin Fc fragment
Glucagon infusion
Glucagón
Hidrocortisona (comprimido de liberacion modificada)
Hormona de crecimiento humana recombinante modificada por fusion de dos cadenas polipetidicas hidrofilicas
Hormona paratiroide recombinante humana
Hydroxypioglitazone
Iobenguane sulfate I 131
Leuprolide acetato
Lipasa lisosomal ácida recombinante humana
Lomitapida
Lonapegsomatropin
Long-acting carboxy-terminal peptide (CTP)-modified human growth hormone (hGH-CTP)
Long-acting recombinant human Growth Hormone (LAPS-rhGH)
Mavoglurant
Mecasermin
Mecasermin rinfabate
Melatonina
Metreleptin
N-[(1R)-1-phenylethyl]-6-{1H-pyrazolo[3,4-d]pyrimidin-4-yl}quinazolin-2-amine
N-[2,6-bis(1-metiletil)fenil]-N'-[[1-[4-(dimetilamino) fenil]ciclopentil]metil]urea, sal clorhidrato
Oligonucleótido fosforotioato anti apolipoproteína C-III
Oxitocina
Peptidomimetic analog of hexarelin
Pioglitazona
Propranolol
Pyrazolo[1,5-a]pyrimidine, 3-[4-chloro-2-(4-morpholinyl)-5-thiazolyl]-7-(1-ethylpropyl)-2,5-dimethyl-pyrazolo[1,3-a]pyrimidine
Pyridoxine and L-pyroglutamic acid
R-baclofeno
Recombinant human ectonucleotide pyrophosphatase/phosphodiesterase 1 fused to the Fc fragment of IgG1
Recombinant human insulin-like growth factor-I/recombinant human insulin-like growth factor binding protein-3
Recombinant human lecithin cholesterol acyltransferase
Recombinant human monoclonal antibody to insulin receptor
Rosuvastatin
Setmelanotide
Somapacitan
Somatropina recombinante
Synthetic cyclic 8 amino acid analogue of human unacylated ghrelin
Temsirolimus
Teriparatide
Tiratricol
Trans-4-[4-[5-[[6-(trifluoromethyl)-3-pyridinyl]amino]-2-pyridinyl]phenyl] cyclohexane acetic acid sodium salt
Triheptanoína
Trofinetide
Valproato sodico
p38 mitogen-activated kinase inhibitor
verucerfont
Ácido 3,5-Diiodotiropropiónico