Orphanet: Búsqueda de un medicamento huérfano
Búsqueda de un medicamento huérfano
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(2R,3S)-2-(4-cyclopentylaminophenyl)-1-(2-fluoro-6-methylbenzoyl)piperidine-3-carboxylic acid(4-methyl-3-trifluoromethylphenyl)amide (R)-1-(2,2-difluorobenzo [d][1,3] dioxol-5-yl)-N-(1-(2,3-dihydroxypropyl)-6-fluoro-2-(1-hydroxy-2-methylpropan-2-yl)-1H-indol-5-yl) cyclopropanecarboxamide (R)-2-(5-cyano-2-(6-(methoxycarbonyl)-7-methyl-3-oxo-8-(3-(trifluoromethyl)phenyl)-2,3,5,8-tetrahydro-[1,2,4]triazolo[4,3-a]pyrimidine-5-yl)phenyl)-N,N,N-trimethylethanaminium methanesulfonate dehydrate (S)-(-)-3-(4-aminophenyl)-2-methoxypropanoic acid (S)-3-((3-(1-((6-((3,4-dimethoxyphenyl)pryazin-2-yl)amino)ethyl)phenyl)carbamoyl)-5-methylpridin-1-ium (S)-8-{2-Amino-6-[1-(5-chloro-biphenyl-2-yl)-(R)-2,2,2-trifluoro-ethoxy]-pyrimidin-4-yl}-2,8-diaza-spiro[4.5]decane-3-carboxylic acid ethyl ester 1,5-(Butylimino)-1,5-dideoxy, D-glucitol 1-(2,2-difluoro-1,3-benzodioxol-5-il)-N-{1-[(2R)-2,3-dihidroxipropil]-6-fluoro-2-(1-hidroxi-2-metilpropano-2-il)-1H-indol-5-il}ciclopropancarboxamida 11-(4-Dimetilamino-3-hidroxi-6-metil-tetrahidro-piran-2-iloxyi)-2-etil-3,4,10-trihidroxi-3,5,6,8,10,12,14-heptametil-1-oxa-6-aza-ciclopentadecano-13,15-dione 2-((2-ethyl-6-(4-(2-(3-hydroxyazetidin-1-yl)-2-oxoethyl)-piperazin-1-yl)-8-methylimidazo[1,2-alpha]pyridin-3-yl)-(methyl)amino)-4-(4-fluorophenyl)-thiazole-5-carbonitrile 2-(2-clorofenil)-4-[3-(dimetilamino)fenil]-5-metil-1H-pirazol [4,3-c]piridina-3,6(2H, 5H)-diona 2-(7-ethoxy-4-(3-fluorophenyl)-1-oxophthalazin-2(1H)-yl)-N-methyl-N-(2-methylbenzo[d]oxazol-6-yl) acetamide 2-hidroxipropil-beta-ciclodextrina 2-{4-[(5,6-diphenylpyrazin-2-yl)(isopropyl)amino]butoxy}-N-(methylsulfonyl)acetamide 2-{[(1r,4r)-4-(((4-chlorophenyl)(phenyl)carbamoyloxy)methyl)cyclohexy]methoxy} acetic acid 3-Pentylbenzeneacetic acid sodium salt 3-[4-(1H-imidazol-1-ylmethyl)phenyl]-5-(2-methylpropyl)thiophene-2-[(N-butyloxylcarbamate)-sulphonamide] sodium salt 4,6,4' - trimetilangelicina 4-[[(1S,4S)-5-[[4-[4-(oxazol-2-yl)phenoxy]phenyl]methyl]-2,5-diazabicyclo[2.2.1]hept-2-yl]methyl]benzoic acid 4-[[9-[(3S)-tetrahidro-3-furanil]-8-[(2,4,6-trifluorofenil)amino]-9H-purin-2-il]amino]-trans-ciclohexanol 6'-(R)-methyl-5-O-(5-amino-5,6-dideoxy-alpha-L-talofuranosyl)-paromamine sulfate 8-cyclopentlyl-1,3-dipropylxanthine ADN plasmídico codificante para el gen humano regulador de la conductancia transmembrana de la fibrosis quística en forma de complejo con un agente de transferencia génica no viral basado en lípidos catiónicos Acetato de sal de ciclo[L-alanil-L-seril-L-isoleucil-L-proliil-L-prolil-L-glutaminil-L-lisil-L-tirosil-D-prolil-L-prolil-(2S)-2-aminodecanoil-L-alfa-glutamil-L-treonil] Acetylcysteine Acetylleucine Adalimumab Alginate oligosaccharide (G-block) fragment Alglucerasa Alpha-1 antitrypsin (inhalation use) Alpha-1 proteinase inhibitor (inhalation use) Ambrisentán Amikacin sulfate (liposomal) Amiloride hydrochloride dihydrate Antagonist of the complement 5a receptor Anti-alfa v beta 6 anticuerpo monoclonal humanizado Anticuerpo recombinante anti-Pseudomonas aeruginosa PcrV Fab' Arimoclomol citrate Ataluren Autologous CD34+ cells transduced with retroviral vector containing the human gp91 (phox) gene Avian polyclonal IgY antibody against Pseudomonas aeruginosa Aviptadil Aztreonam lysinate (inhalation use) Bacterial lipase Beraprost sodico Beraprost sodium (modified release tablet) Bosentan Budesonide (oral use) Carbamic acid, [[4-[[3-[[4-[1-(4-hydroxyphenyl)-1-methylethyl] phenoxy]methyl]phenyl]methoxy]-phenyl]iminomethyl]-,ethyl ester (amelubant) Ceramidase ácido humano recombinante Ciprofloxacina (liposomal) Ciprofloxacina (via inhalatoria) Cisteamina Citrato de sildenafilo Colistimethate sodium Cystic fibrosis transmembrane conductance regulator (CFTR) amplifier Células hematopoyéticas autólogas, genéticamente modificadas con un vector lentiviral que contiene el gen humano gp91(phox) Denufosol tetrasodium Dexamethasone sodium phosphate encapsulated in human erythrocytes Dipalmitoilfosfatidilcolina, 1-palmitoil-2-oleoil-sn-glicero-3-fosfoglicerol, sal sódica, análogo de la proteína C tensioactiva sintética y análogo de la proteína B tensioactiva sintética Dornase alfa Drotrecogin alfa (activated) Duramycin Elafin Eliglustat Engineered protein inhibitor of human neutrophil elastase Epoprostenol Etanercept Factor estimulador de colonias de granulocitos-macrófagos Fixed-dose combination of fosfomycin disodium and tobramycin Gallium citrate Givinostat Glutathione Gusperimus trihydrochloride Heparin sodium Hypothiocyanitos / lactoferrina Iloprost Iloprost inhalation solution Iloprost trometamol Imatinib mesilato Imiglucerasa Immunoglobulin G-degrading enzyme of Streptococcus pyogenes Interferon beta Interferon gamma 1A Interferon gamma 1B Interferón gamma L-Lysine-N-acetyl-L-cysteinate L-Pir-L-Glu-L-Gln-L-Leu-L-Glu-L-Arg-L-Ala-L-Leu-L-Asn-L-Ser-L-Ser Levofloxacin hemihydrate Lucinactant Lumacaftor / Ivacaftor Lusupultide Macitentan Maleato de hidrógeno de lisurida Mannitolum Meloxicam Mepolizumab Mesilato de nafamostat Methyl 4,6-diamino-2-[1-(2-fluorobenzyl)-1H-pyrazolo[3,4-b]pyridine-3-yl]-5-pyrimidinyl(methyl)carbamate Microvesícula multilamelar que comtiene fosfatidilcolina, esfingomielina, fosfatidiletanolamina, fosfatidilserina, fosfatidilinositol y colesterol Molgramostim N-(2,4-Di-tert-butyl-5-hydroxyphenyl)-1,4-dihydro-4-oxoquinoline-3-carboxamide N-(tert-butylcarbamoyl)-5-cyano-2-((4'-(difluoromethoxy)-[1,1'-biphenyl]-3-yl)oxy)benzenesulfonamide Nintedanib Nitrito de sodio Nitrogeno monoxido de Octovalent Pseudomonas aeruginosa O-polysaccharie-toxin A conjugate vaccine Oligonucleótido antisentido dirigido a la mutación delta F508 del CFTR Pancreatic enzymes (cross linked enzyme crystal lipase, protease, amylase) Phosphoinositide 3-kinase gamma peptide Pirfenidone Proteína 70 del shock térmicorecombinante humana Pulmonary surfactant replacement, porcine Ralinepag RecoCXCL8 mutante recombinante humano Recombinant dog gastric lipase Recombinant human acid sphingomyelinase Recombinant human bile salt-stimulated lipase Recombinant human club cell 10 KDa protein (rhCC10) Recombinant human monoclonal antibody against mannan-binding lectin-associated serine protease-2 Recombinant human monoclonal antibody against transforming growth factor beta-1, 2 and 3 Recombinant human monoclonal antibody to human IL-1beta of the IgG1/K class Recombinant human pentraxin-2 Recombinant microbial lipase Resunab Riociguat Rituximab Sinapultida, dipalmitoilfosfatidilcolina, palmitoiloleoilfosfatidilglicerol y acido palmitico Sirolimus (Rapamycin) Sitaxentan sodium Sodium cromoglicate Sulfato de amikacina Surface active extract of saline lavage of bovine lungs T-Cell Depleted Stem Cell Enriched Cellular Product From Peripheal Blood Stem Cells Tacrolimus Tamoxifen citrate Teicoplanin Temocillin sodium Tergurida Tezacaftor / Ivacaftor Tipelukast Tobramicina (liposomal) Tobramicina (via inhalatoria) Tobramycin (inhalation powder) Tobramycin (inhalation solution) Tocilizumab Tralokinumab Treprostinil diethanolamine (oral use) Treprostinil sodium Ubenimex Ursodeoxicolico acido Vasoactive intestinal peptide (VIP)-elastin-like peptide (ELP) fusion protein adeno-associated viral vector serotype 9 containing the human glucocerebrosidase gene codon-optimised human cystic fibrosis transmembrane conductance regulator messenger ribonucleic acid complexed with lipid-based nanoparticles ivacaftor, N-(1,3-dimethyl-1H-pyrazole-4-sulfonyl)-6-[3-(3,3,3-trifluoro-2,2-dimethylpropoxy)-1H-pyrazol-1-yl]-2-[(4S)-2,2,4-trimethylpyrrolidin-1-yl]pyridine-3-carboxamide, tezacaftor ivacaftor, potassium(benzenesulfonyl)({[6-(3-{2-[1-(trifluoromethyl) cyclopropyl]ethoxy}-1H-pyrazol-1-yl)-2-[(4S)-2,2,4-trimethylpyrrolidin-1-yl]pyridin-3-yl]carbonyl})azanide, tezacaftor poly-N (acetyl, arginyl) glucosamine (PAAG) sodium nitrite and ethylenediaminetetraacetic acid tilorone Ácido 3-(6-(1-(2,2-difluorobenzo [d] [1,3]dioxol-5-yl)ciclopropanocarboxamido)-3-metilpiridin-2-il) benzoico
