Búsqueda de un medicamento huérfano
Otra(s) opcion(es) de búsqueda
20 Resultado(s)
Principio(s) activo(s)
- (Z)-3-(3-(3,5-bis(trifluorometil)fenil-1H-1,2,4-triazol-1-il)-N'-(pirazin-2-il)acrilhidrazida
- Adeno-associated viral vector serotype 8 containing the human alpha-galactosidase A gene
- Adeno-associated viral vector serotype S3 encoding human alpha-galactosidase A cDNA
- Adeno-associated virus serotype C102 containing the human GLA gene
- Agalsidase alfa
- Agalsidase beta
- Allogeneic multi-virus specific T lymphocytes targeting BK virus, cytomegalovirus, human herpesvirus-6, Epstein Barr virus and adenovirus
- Alpha galactosidase A
- Autologous CD34+ cells transduced with a lentiviral vector encoding galactosidase alpha
- Besilesomab
- Lucerastat
- Migalastat hydrochloride
- Pegunigalsidase alfa
- adeno-associated virus serotype 2/6 encoding human alpha-galactosidase A cDNA
- haematopoietic stem cells and blood progenitors umbilical cord-derived expanded with (1R, 4R)-N1-(2-benzyl-7-(2-methyl-2H-tetrazol-5-yl)-9H-pyrimido[4,5-b]indol-4-yl)cyclohexane-1,4-diamine dihydrobromide dihydrate