Substance(s)

• 1,5-(Butylimino)-1,5-dideoxy, D-glucitol
• 1-deoxynojirimycin hydrochloride
• Adeno-associated viral vector serotype 8 containing the human acid alpha-glucosidase gene
• Alglucosidase alfa.
• Alpha-glucosidase acide recombinante humaine marquée à la GILT
• Alpha-glucosidase recombinante humaine conjuguée à de multiples copies de bis-mannose-6-phosphate-tétra-mannose-glycane de synthèse
• Clenbuterol
• Recombinant adeno-associated viral vector containing a bioengineered capsid serotype AAV-rh74 and a codon-optimised expression cassette to drive the expression of a secretable form of human acid alpha-glucosidase
• Recombinant adeno-associated viral vector containing human acid alfa-glucosidase-gene
• Recombinant human acid alpha-glucosidase
• Recombinant human acid alpha-glucosidase conjugated with mannose-6-phosphate analogues
• Triheptanoïne
• Valproic acid, sodium
• adeno-associated viral vector serotype 8 containing the human glucose-6-phosphatase gene

Nom(s) commercial(aux)

• LUMIZYME
• MYOZYME