Sostanza(e)

• 1,5-(Butylimino)-1,5-dideoxy, D-glucitol
• 1-deoxynojirimycin hydrochloride
• Adeno-associated viral vector serotype 8 containing the human acid alpha-glucosidase gene
• Alfa glucosidasi acida umana ricombinante GILT-marcata
• Alfa-glucosidasi umana ricombinante coniugata con copie multiple di bis-mannosio-6-fosfato-tetra mannosio glicano di sintesi
• Alglucosidase alfa
• Clenbuterol
• Recombinant adeno-associated viral vector containing a bioengineered capsid serotype AAV-rh74 and a codon-optimised expression cassette to drive the expression of a secretable form of human acid alpha-glucosidase
• Recombinant adeno-associated viral vector containing human acid alfa-glucosidase-gene
• Recombinant human acid alpha-glucosidase
• Recombinant human acid alpha-glucosidase conjugated with mannose-6-phosphate analogues
• Trieptanoina
• Valproic acid, sodium
• adeno-associated viral vector serotype 8 containing the human glucose-6-phosphatase gene

Nome(i) commerciale(i)

• LUMIZYME
• MYOZYME