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(2S)-2-{[(2R)-2-[({[3,3-dibutyl-7-(methylthio)-1,1-dioxido-5-phenyl-2,3,4,5-tetrahydro-1,2,5-benzothiadiazepin-8-yl]oxy}acetyl)amino]-2-(4-hydroxyphenyl)acetyl]amino}butanoic acid
(4R,5R)-1-[[4-[[4-[3,3-dibutil-7-(dimetilammino)-2,3,4,5-tetraidro-4-idrossi-1,1-diossido-1-benzotiepina-5-il]fenossi]metil]fenil]metil]-4-aza-1-azoniabiciclo[2.2.2]ottano cloruro
8-[4-(1-aminociclobutil)fenil]-9-fenil-1,2,4-triazolo[3,4-f][1,6]naftiridin-3(2H)-one monocloridrato
Abagovomab
Acetylleucine
Acido eicosapentaenoico
Adenoviral vector containing human p53 gene
Afatinib
Anticorpo monoclonale anti-EphA2 coniugato a maleimidocaproil, monometilauristatin-fenilalanina
Autologous CD34+ cells transduced with the W1.6_hWASP_WPRE lentiviral vector
Bacterial lipase
Cannabidiolo
Celecoxib
Cellule CD34+ autologhe transfettate con vettore lentivirale contenente il gene umano della proteina della sindrome di Wiskott Aldrich
Dexamethasone sodium phosphate encapsulated in human erythrocytes
Doxorubicin hydrochloride (pegylated liposomal)
Eflornithine hydrochloride
Eflornitina
Eflornitina in combinazione con sulindac
Everolimus
Gefitinib
Imexon
Itraconazole
Lentiviral vector containing the human Wiskott Aldrich syndrome protein gene
Mibefradil
Miransertib
Mirdametinib
N-[6-(cis-2,6-dimetilmorfolin-4-il)piridin-3-il]-2-metil-4'-(trifluorometossi)[1,1'-bifenil]-3-carbossamide
N-idrossi-4-(3-metil-2-(S)-fenil-butyrylamino) benzamide
Nitisinone
Pancreatic enzymes (cross linked enzyme crystal lipase, protease, amylase)
Patidegib
Patupilone
Pir-His-Trp-Ser-Tir-D-Lis(doxorubicinilglutarato)-Leu-Arg-Pro-Gli-NH2, acetato
Plevitrexed
Propranolol
Recombinant human dyskerin
Recombinant microbial lipase
Selumetinib
Sirolimus (Rapamycin)
Treosulfan
Valproic acid, sodium
Vettore lentivirale contenente il gene dell'anemia di Fanconi A (FANCA)
[5,10,15,20-tetrakis(4-carboxyphenyl)-21H,23H-porphine]manganese(III) chloride