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- (2R,3S)-2-(4-cyclopentylaminophenyl)-1-(2-fluoro-6-methylbenzoyl)piperidine-3-carboxylic acid(4-methyl-3-trifluoromethylphenyl)amide
- 1,5-(Butylimino)-1,5-dideoxy, D-glucitol
- 2-idrossipropil-beta-ciclodestrina
- Acetylleucine
- Alglucerase
- Antagonist of the complement 5a receptor
- Arimoclomol citrate
- Eliglustat
- Gusperimus trihydrochloride
- Imiglucerasa
- Immunoglobulin G-degrading enzyme of Streptococcus pyogenes
- Mepolizumab
- Proteina dello shock termico 70 umanaricombinante
- Rituximab
- Ursodeoxycholic acide
- adeno-associated viral vector serotype 9 containing the human glucocerebrosidase gene