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(3S)-(+)-(5-chloro-2-methoxyphenyl)-1,3-dihydro-3-fluoro-6-(trifluoromethyl)-2H-indol-2-uno (R)-3-(1-(2,3-dichloro-4-(pyrazin-2-yl)phenyl)-2,2,2-trifluoroethyl)-1-methyl-1-(1-methylpiperidin-4-yl)urea fumarate (S)-1-(4-(1-(3,4,5-trimethoxyphenyl)-1H-imidazol-4-ylamino)thieno[2,3-d]pyrimidin-2-yl)pyrrolidine-2-carboxamide 2'-O-(2-methoxyethyl) modified antisense oligonucleotide targeting UBE3A antisense transcript RNA 2-[4-[3-(methylamino)-1-phenylpropoxy]phenyl]ethanol hydrochloride 4-(3-cyano-6-ethoxyquinolin-2-yl)-N- (2-fluorophenyl)-1,4-diazepane-1-carbothiomide 4-(6-(4-(piperazin-1-yl)phenyl_pyrazolo[1,5-a]pyrimidin-3-yl)quinoline hydrochloride 4-benzil-2-naftalen-1-il-1,2,4-tiadiazolidin-3,5-dione 5-{(1R,2R)-2-[(cyclopropylmethyl)amino]cyclopropyl}-N-(tetrahydro-2H-pyran-4-yl)thiophene-3-carboxamide monohydrochloride Acebutolol Adeno-associated virus serotype PTC3 expressing the human UBE3A gene Afatinib Allogeneic cultured postnatal thymus-derived tissue Alpha-tocopherol and ascorbic acid Bacterial lipase Balipodect Beloranib Blarcamesine Calcio acamprosate Cannabidiol acid methyl ester Cannabidiolo Cannabidivarin Carbetocina Codergocrine mesilate, oxitriptan Davunetide Diazoxide choline Gaboxadol monohydrate Gefitinib Human monoclonal antibody against activin A IPN-60130 Ibudilast Lisuride Maleate Lyophilized microbiota purified from the stool of screened, healthy human donors Mavoglurant Melatonina Metreleptin N-[(1R)-1-phenylethyl]-6-{1H-pyrazolo[3,4-d]pyrimidin-4-yl}quinazolin-2-amine Ossitocina Palovarotene Pancreatic enzymes (cross linked enzyme crystal lipase, protease, amylase) Psilocybine Pyridoxine and L-pyroglutamic acid R-baclofene Recombinant adeno-associated viral vector serotype 9 carrying the gene for the human E6-AP ubiquitin protein ligase Recombinant microbial lipase Replication-incompetent adeno-associated virus serotype 9 vector encoding the human fragile x mental retardation 1 gene Setmelanotide Somatotropina ricombinante Sulindac Synthetic cyclic 8 amino acid analogue of human unacylated ghrelin Synthetic oligonucleotide selectively targeting UBE3A antisense RNA transcripts Trofinetide Vettore lentivirale contenente il gene dell'anemia di Fanconi A (FANCA) [5,10,15,20-tetrakis(4-carboxyphenyl)-21H,23H-porphine]manganese(III) chloride cyclo-L-glycyl-L-2-allylproline
