Orphanet: Search for an orphan drug
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87 Resultaat/Resultaten
(5R,5aR,8aR,9S)-9-[[4,6-O-[(R)-Ethylideen]-beta-D-glucopyranosyl]-oxy]-5-(4-({[(2,2-dimethyl-1,3-dioxolaan-4-yl)methoxy]carbonyl}oxy)-3,5-dimethoxyfenyl)-5,8,8a,9-tetrahydro-isobenzofuro[5,6-f][1,3]benzodioxol-6(5aH)-one (R) -6-(2-fluorophenyl) -N-(3-(2-((2 -methoxyethyl)amino)ethyl)phenyl)-5,6 - dihydrobenzo[h]quinazolin -2-amine dihydrochlorid (S)-10-[(dimethylamino)methyl]-4-ethyl-9-hydroxy-4-O-[alpha-(2'', 4'', 5'', 7''- tetranitro-9''-fluorenylideneaminooxy)propionyl]-1H-pyrano[3', 4', 6', 7']indolizino[1,2- beta]-quinoline-3, 14-(4H, 12H)-dione, hydrochloride 1-((2S,4S)-2-((((S)-(4-bromophenoxy)(((S)-1-oxo-1-(((S)-pentan-2-yl)oxy)propan-2-yl)amino)phosphoryl)oxy)methyl)-1,3-dioxolan-4-yl)-2-oxo-1,2-dihydropyrimidin-4-aminium chloride 2-(2-phenylvinyl)-4-[4-methylpiperazin-1-yl)]-6-(5-methyl-2H-pyrazol-3-yl-amino)-pyrimidine L(+) tartrate salt 2-Chloro-N6-(3-iodobenzyl)adenosine-5'-N-methyluronamide 4-Amino-1-[5-O-[(2R,4S)-2-oxido-4-(4-pyridinyl)-1,3,2-dioxaphosphorinan-2-yl]-D-arabinofuranosyl]- 2(1H)-pyrimidinone 4-[2-(6-methylpyridine-2-yl)-5,6-dihydro-4H-pyrrolo[1,2-b]pyrazol-3-yl]-chinoline-6-carboxamide monohydraat 4-[3,5-bis(trimethylsilyl)benzamido] benzoic acid 5,10,15,20-tetrakis(2,6-difluoro-3-N-methylsulfamoylphenyl) bacteriochlorin 5-amino-1-(2-methyl-1H-benzo[d]imidazol-5-yl)-1H-pyrazol-4-yl 1H-indol-2-yl ketone mono[(S)-2-hydroxysuccinate] 6-thio-2'-deoxyguanosine A genetically modified Salmonella comprising of methioninase An autologous T-cell immunotherapy (ET140203) Becatecarin Bicistronic messenger ribonucleic acid (mRNA) encoding for ZF-DNMT and ZF-KRAB proteins, encapsulated in a lipid nanoparticle (LNP) Bifunctional anti-PD-L1/TGFβ Trap fusion protein Brivanib alaninate Devimistat Diaspirin cross-linked haemoglobin Doxorubicin carbon/iron magnetically targeted microparticles Doxorubicin hydrochloride (in heat-sensitive liposomes) Doxorubicin polyisohexylcyanoacrylate nanoparticles Ethiodized oil injection Ezurpimtrostat Fibroblast growth factor receptor (FGFR) inhibitor Fimaporfin Florilglutamic acid (18F) Fosgemcitabine palabenamide Futibatinib IgG1 humanized antibody directed against Carcinoembryonic Antigen-related Cell Adhesion Molecule (CEACAM)1, 3 and 5 Infigratinib Ivosidenib Lenvatinib Mefuparib Mertansine functionalised gold nanoconjugate Mifamurtide N- 1',2-dihydroxy- 1,2'-binapthalen -4'-yl -4-methoxybenzenesulfonamide N-(4-(4-amino-5-(3-fluoro-4-((4-methylpyrimidin-2-yl)oxy)phenyl)-7-methyl-7H-pyrrolo[2,3-d]pyrimidin-6-yl)phenyl)methacrylamide hydrochloride N-(6-(2,6-dichloro-3,5-dimethoxyphenyl)-1H-pyrazolo[3,4-b]pyridin-3-yl)-4-(3,3-dimethylpiperazin-1-yl)benzamide hydrochloride N-[4-(3-amino-1H-indazol-4 yl)phenyl]-N'-(2-fluoro-5-methylphenyl) urea N-{2-[(6-{[(2,6-dichloro-3,5-dimethoxyphenyl)carbamoyl](methyl)amino}pyrimidin-4-yl)amino]-5-(4-ethylpiperazin-1-yl)phenyl}prop-2-enamide NGR-human Tumour Necrosis Factor Nanvuranlat Nemorubicin hydrochloride Nolatrexed Pegylated arginine deiminase Peretinoin Porfimer sodium (for use with photodynamic therapy) Ramucirumab Recombinant human IL12/15-PDL1B HSV-1 oncolytic virus Injection Recombinant oncolytic virus M1-c6v1 Rencofilstat Resminostat Seocalcitol Silmitasertib Sorafenib Sulfonated monophosphorylated mannose oligosaccharide Tegavivint Thymalfasin Tirapazamine Tislelizumab Tivantinib Tremelimumab Vaccinia GM-CSF/TK-deactivated virus Veliparib a humanized immunoglobulin IgG1 antibody with a kappa light chain (LC) which has high selectivity and specificity for cancer-specific plectin an autologous T-cell immunotherapy (ECT204) sodium 2-hydroxylinoleate zanidatamab
