Orphanet: Wyszukaj lek sierocy
Wyszukaj lek sierocy
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- (R)-1-(2,2-difluorobenzo [d][1,3] dioxol-5-yl)-N-(1-(2,3-dihydroxypropyl)-6-fluoro-2-(1-hydroxy-2-methylpropan-2-yl)-1H-indol-5-yl) cyclopropanecarboxamide
- (R)-2-(5-cyano-2-(6-(methoxycarbonyl)-7-methyl-3-oxo-8-(3-(trifluoromethyl)phenyl)-2,3,5,8-tetrahydro-[1,2,4]triazolo[4,3-a]pyrimidine-5-yl)phenyl)-N,N,N-trimethylethanaminium methanesulfonate dehydrate
- (S)-(-)-3-(4-aminophenyl)-2-methoxypropanoic acid
- (S)-8-{2-Amino-6-[1-(5-chloro-biphenyl-2-yl)-(R)-2,2,2-trifluoro-ethoxy]-pyrimidin-4-yl}-2,8-diaza-spiro[4.5]decane-3-carboxylic acid ethyl ester
- 11-(4-Dimethylamino-3-hydroxy-6-methyl-tetrahydro-pyran-2-yloxy)-2-ethyl-3,4,10-trihydroxy-3,5,6,8,10,12,14-heptamethyl-1-oxa-6-aza-cyclopentadecane-13,15-dione
- 2-((2-ethyl-6-(4-(2-(3-hydroxyazetidin-1-yl)-2-oxoethyl)-piperazin-1-yl)-8-methylimidazo[1,2-alpha]pyridin-3-yl)-(methyl)amino)-4-(4-fluorophenyl)-thiazole-5-carbonitrile
- 2-(2-chlorophenyl)-4-[3-(dimethylamino)phenyl]-5-methyl-1H-pyrazolo[4,3-c]pyridine-3,6(2H,5H)-dione
- 2-(7-ethoxy-4-(3-fluorophenyl)-1-oxophthalazin-2(1H)-yl)-N-methyl-N-(2-methylbenzo[d]oxazol-6-yl) acetamide
- 2-{[(1r,4r)-4-(((4-chlorophenyl)(phenyl)carbamoyloxy)methyl)cyclohexy]methoxy} acetic acid
- 3-(6-(1-(2,2-difluorobenzo [d] [1,3] dioxol-5-yl)cyclopropanecarboxamido)-3- methylpyridin-2-yl)benzoic acid
- 3-Pentylbenzeneacetic acid sodium salt
- 3-[4-(1H-imidazol-1-ylmethyl)phenyl]-5-(2-methylpropyl)thiophene-2-[(N-butyloxylcarbamate)-sulphonamide] sodium salt
- 4,6,4'-trymethylangelicin
- 4-[[(1S,4S)-5-[[4-[4-(oxazol-2-yl)phenoxy]phenyl]methyl]-2,5-diazabicyclo[2.2.1]hept-2-yl]methyl]benzoic acid
- 6'-(R)-methyl-5-O-(5-amino-5,6-dideoxy-alpha-L-talofuranosyl)-paromamine sulfate
- 8-cyclopentyl-1,3-dipropylxanthine
- Acetylcysteine
- Adrenomedullin
- Alginate oligosaccharide (G-block) fragment
- Allogeneic ex-vivo-expanded human umbilical cord blood-derived mesenchymal stem cells
- Alpha-1 antitrypsin (inhalation use)
- Alpha-1 proteinase inhibitor
- Alpha-1 proteinase inhibitor (inhalation use)
- Ambrisentan
- Amikacin sulfate
- Amikacin sulfate (liposomal)
- Amiloride hydrochloride dihydrate
- Amphotericin B (for inhalation use)
- Asp-Arg-Val-Try-Ile-His-Pro
- Ataluren
- Avian polyclonal IgY antibody against Pseudomonas aeruginosa
- Aviptadil
- Aztreonam lysinate (inhalation use)
- Bacterial lipase
- Beraprost sodium
- Beraprost sodium (modified release tablet)
- Bevacizumab
- Bimosiamose disodium
- Bosentan
- Caffeine citrate
- Carbamic acid, [[4-[[3-[[4-[1-(4-hydroxyphenyl)-1-methylethyl] phenoxy]methyl]phenyl]methoxy]-phenyl]iminomethyl]-,ethyl ester
- Ciprofloxacin (inhalation use)
- Ciprofloxacin (liposomal)
- Clofazimine
- Colistimethate sodium
- Cyclo-Cys-Gly-Gln-Arg-Glu-Thr-Pro-Glu-Gly-Ala-Glu-Ala-Lys-Pro-Trp-Tyr-Cys
- Cyclo[L-alanyl-L-seryl-L-isoleucyl-L-prolyl-L-prolyl-L-glutaminyl-L-lysyl-L-tyrosyl-D-prolyl-L-prolyl-(2S)-2-aminodecanoyl-L-alpha-glutamyl-L-threonyl] acetate salt
- Cysteamine
- Cystic fibrosis transmembrane conductance regulator (CFTR) amplifier
- Denufosol tetrasodium
- Dexamethasone sodium phosphate encapsulated in human erythrocytes
- Dipalmitoylphosphatidylcholine, 1-palmitoyl-2-oleoyl-sn-glycero-3-phosphoglycerol, sodium salt, synthetic surfactant protein C analogue and synthetic surfactant protein B analogue
- Dornase alfa
- Doxophylline
- Drotrecogin alfa (activated)
- Duramycin
- Elafin
- Elexacaftor/Tezacaftor/Ivacaftor
- Eluforsen
- Engineered protein inhibitor of human neutrophil elastase
- Epoprostenol
- Estradiol hemihydrate and Progesterone
- Etamsylate
- Fixed-dose combination of fosfomycin disodium and tobramycin
- Gallium citrate
- Glutathione
- Granulocyte-macrophage colony-stimulating factor
- Heparin sodium
- Human alpha 1-antitrypsin
- Human alpha1-proteinase inhibitor (respiratory use)
- Human monoclonal antibody against Pseudomonas aeruginosa IATS-O1
- Human monoclonal antibody against Pseudomonas aeruginosa serotype O11
- Human monoclonal antibody targeting Staphylococcus aureus alpha-toxin
- Human tumour necrosis factor alfa-derived peptide Cys-Gly-Gln-Arg-Glu-Thr-Pro-Glu-Gly-Ala-Glu-Ala-Lys-Pro-Trp-Tyr-Cys
- Humanised anti-alpha v beta 6 monoclonal antibody
- Hypothiocyanite / lactoferrin
- Iloprost
- Iloprost inhalation solution
- Iloprost trometamol
- Imatinib mesilate
- Interferon beta
- Interferon gamma
- Interferon gamma 1b
- Ivacaftor
- L-Lysine-N-acetyl-L-cysteinate
- L-Pyr-L-Glu-L-Gln-L-Leu-L-Glu-L-Arg-L-Ala-L-Leu-L-Asn-L-Ser-L-Ser
- Lenabasum
- Liprotamase
- Lisuride hydrogen maleate
- Lucinactant
- Lumacaftor / Ivacaftor
- Lusupultide
- Macitentan
- Mannitolum
- Methyl 4,6-diamino-2-[1-(2-fluorobenzyl)-1H-pyrazolo[3,4-b]pyridine-3-yl]-5-pyrimidinyl(methyl)carbamate
- Molgramostim
- Multilamellar microvesicle comprising phosphatidylcholine, sphingomyelin, phosphatidylethanolamine, phosphatidylserine, phosphatidylinositol and cholesterol
- N-(tert-butylcarbamoyl)-5-cyano-2-((4'-(difluoromethoxy)-[1,1'-biphenyl]-3-yl)oxy)benzenesulfonamide
- N-acetylgalactosamine-conjugated synthetic double-stranded oligomer specific to serpin family A member 1 gene
- Nafamostat mesilate
- Nintedanib
- Nitric oxide
- Octovalent Pseudomonas aeruginosa O-polysaccharie-toxin A conjugate vaccine
- Pegylated recombinant anti-Pseudomonas aeruginosa PcrV Fab' antibody
- Phosphoinositide 3-kinase gamma peptide
- Pirfenidone
- Plasmid DNA encoding the human cystic fibrosis transmembrane conductance regulator gene complexed with a non-viral, cationic lipid based gene transfer agent
- Platelet-derived growth factor (PDGF) receptor kinase inhibitor
- Porcine lung surfactant
- Pulmonary surfactant replacement, porcine
- Ralinepag
- Raloxifene hydrochloride
- Recombinant adeno-associated viral vector containing human alpha-1 antitrypsin gene
- Recombinant coagulation factor VIIa (rFVIIa)
- Recombinant dog gastric lipase
- Recombinant fragment of human surfactant protein-D (rfhSP-D)
- Recombinant human CXCL8 mutant
- Recombinant human acid ceramidase
- Recombinant human alpha-1-antitrypsin (respiratory use)
- Recombinant human bile salt-stimulated lipase
- Recombinant human club cell 10 KDa protein (rhCC10)
- Recombinant human monoclonal antibody against transforming growth factor beta-1, 2 and 3
- Recombinant human pentraxin-2
- Recombinant human surfactant protein D
- Recombinant microbial lipase
- Retinol
- Riociguat
- Selexipag
- Sildenafil citrate
- Sinapultide, dipalmitoylphosphatidylcholine, palmitoyloleoylphosphatidylglycerol and palmitic acid
- Single-chain urokinase plasminogen activator
- Sirolimus
- Sitaxentan sodium
- Sodium cromoglicate
- Sodium nitrite
- Surface active extract of saline lavage of bovine lungs
- Synthetic double-stranded oligomer specific to the SERPINA1 gene and containing a cholesterol-conjugated, acyclic nucleobase analogue
- Synthetic double-stranded siRNA oligonucleotide directed against SERPINA1 mRNA and containing four modified nucleosides which form a ligand cluster of four N-acetylgalactosamine residues
- Tacrolimus
- Tamoxifen citrate
- Tanzisertib
- Teicoplanin
- Temocillin sodium
- Terguride
- Tezacaftor
- Tezacaftor / Ivacaftor
- Thalidomide
- Tilorone
- Tipelukast
- Tobramycin (inhalation powder)
- Tobramycin (inhalation solution)
- Tobramycin (inhalation use)
- Tobramycin (liposomal)
- Tralokinumab
- Treprostinil diethanolamine (oral use)
- Treprostinil sodium
- Treprostinil sodium (inhalation use)
- Ubenimex
- Vasoactive intestinal peptide (VIP)-elastin-like peptide (ELP) fusion protein
- codon-optimised human cystic fibrosis transmembrane conductance regulator messenger ribonucleic acid complexed with lipid-based nanoparticles
- imlifidase
- interferon alfa-n3
- ivacaftor, potassium(benzenesulfonyl)({[6-(3-{2-[1-(trifluoromethyl) cyclopropyl]ethoxy}-1H-pyrazol-1-yl)-2-[(4S)-2,2,4-trimethylpyrrolidin-1-yl]pyridin-3-yl]carbonyl})azanide, tezacaftor
- levofloxacin hemihydrate
- poly-N (acetyl, arginyl) glucosamine (PAAG)
- sodium nitrite and EDTA
