Orphanet: Wyszukaj lek sierocy
Wyszukaj lek sierocy
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- (5R,5aR,8aR,9S)-9-[[4,6-O-[(R)-Ethylidene]-beta-D-glucopyranosyl]-oxy]-5-(4-({[(2,2-dimethyl-1,3-dioxolan-4-yl)methoxy]carbonyl}oxy)-3,5-dimethoxyphenyl)-5,8,8a,9-tetrahydroisobenzofuro[5,6-f][1,3]benzodioxol-6(5aH)-one
- (R)-6-(2-fluorophenyl)-N-(3-(2-((2 -methoxyethyl)amino)ethyl)phenyl)-5,6-dihydrobenzo[h]quinazolin-2-amine dihydrochloride
- (S)-10-[(dimethylamino)methyl]-4-ethyl-9-hydroxy-4-O-[alpha-(2'', 4'', 5'', 7''- tetranitro-9''-fluorenylideneaminooxy)propionyl]-1H-pyrano[3', 4', 6', 7']indolizino[1,2- beta]-quinoline-3, 14-(4H, 12H)-dione, hydrochloride
- 1-((2S,4S)-2-((((S)-(4-bromophenoxy)(((S)-1-oxo-1-(((S)-pentan-2-yl)oxy)propan-2-yl)amino)phosphoryl)oxy)methyl)-1,3-dioxolan-4-yl)-2-oxo-1,2-dihydropyrimidin-4-aminium chloride
- 2-(2-phenylvinyl)-4-[4-methylpiperazin-1-yl)]-6-(5-methyl-2H-pyrazol-3-yl-amino)-pyrimidine L(+) tartrate salt
- 4-Amino-1-[5-O-[(2R,4S)-2-oxido-4-(4-pyridinyl)-1,3,2-dioxaphosphorinan-2-yl]-D-arabinofuranosyl]- 2(1H)-pyrimidinone
- 4-[3,5-bis(trimethylsilyl)benzamido] benzoic acid
- 5,10,15,20-tetrakis(2,6-difluoro-3-N-methylsulfamoylphenyl) bacteriochlorin
- 5-amino-1-(2-methyl-1H-benzo[d]imidazol-5-yl)-1H-pyrazol-4-yl 1H-indol-2-yl ketone mono[(S)-2-hydroxysuccinate]
- A genetically modified Salmonella comprising of methioninase
- An autologous T-cell immunotherapy (ET140203)
- Becatecarin
- Bicistronic messenger ribonucleic acid (mRNA) encoding for ZF-DNMT and ZF-KRAB proteins, encapsulated in a lipid nanoparticle (LNP)
- Bintrafusp Alfa
- Brivanib alaninate
- Devimistat
- Diaspirin cross-linked haemoglobin
- Doxorubicin Transdrug
- Doxorubicin carbon/iron magnetically targeted microparticles
- Doxorubicin hydrochloride (in heat-sensitive liposomes)
- Ethiodized oil injection
- Ezurpimtrostat
- Fibroblast growth factor receptor (FGFR) antagonist
- Fibroblast growth factor receptor (FGFR) inhibitor
- Fimaporfin
- Florilglutamic acid (18F)
- Fosgemcitabine palabenamide
- Galunisertib
- Infigratinib
- Ivosidenib
- Lenvatinib
- Mertansine functionalised gold nanoconjugate
- Mifamurtide
- N-(4-(4-amino-5-(3-fluoro-4-((4-methylpyrimidin-2-yl)oxy)phenyl)-7-methyl-7H-pyrrolo[2,3-d]pyrimidin-6-yl)phenyl)methacrylamide hydrochloride
- N-(6-(2,6-dichloro-3,5-dimethoxyphenyl)-1H-pyrazolo[3,4-b]pyridin-3-yl)-4-(3,3-dimethylpiperazin-1-yl)benzamide hydrochloride
- N-[4-(3-amino-1H-indazol-4 yl)phenyl]-N'-(2-fluoro-5-methylphenyl) urea
- N-{2-[(6-{[(2,6-dichloro-3,5-dimethoxyphenyl)carbamoyl](methyl)amino}pyrimidin-4-yl)amino]-5-(4-ethylpiperazin-1-yl)phenyl}prop-2-enamide
- NGR-human Tumour Necrosis Factor
- Namodenoson
- Nemorubicin hydrochloride
- Nolatrexed
- Pegylated arginine deiminase
- Peretinoin
- Porfimer sodium (for use with photodynamic therapy)
- Ramucirumab
- Recombinant oncolytic virus M1-c6v1
- Resminostat
- Seocalcitol
- Sorafenib tosylate
- Sulfonated monophosphorylated mannose oligosaccharide
- Tegavivint
- Thymalfasin
- Tirapazamine
- Tislelizumab
- Tivantinib
- Tremelimumab
- Vaccinia GM-CSF/TK-deactivated virus
- Veliparib
- a humanized immunoglobulin IgG1 antibody with a kappa light chain (LC) which has high selectivity and specificity for cancer-specific plectin
- an autologous T-cell immunotherapy (ECT204)
- sodium 2-hydroxylinoleate
- zanidatamab