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Substancja (substancje)
- Allogeneic cultured postnatal thymus-derived tissue
- Autologous CD34+ cells transfected with a lentiviral vector containing codon optimised RPS19 gene
- Autologous CD34+ enriched cells transduced with a self-inactivating lentiviral vector containing the codon-optimized RPS19 gene
- Cannabidiol
- Miransertib
- Potassium iodide oral solution