Orphanet: Wyszukaj lek sierocy
Wyszukaj lek sierocy
89 Wyniki
(1'R,6'R)-3-(benzylamine)-6-hydroxy-3'-methyl-4-pentyl-6'-(prop-1-en-2-yl)-[1,1'-bi(cyclohexane)]-2',3,6-triene-2,5-dione
2-(2-chlorophenyl)-4-[3-(dimethylamino)phenyl]-5-methyl-1H-pyrazolo[4,3-c]pyridine-3,6(2H,5H)-dione
2-[4-Methoxy-3-(2-m-tolyl-ethoxy)-benzoylamino]-indan-2-carboxylic acid
3-(3-(3,5-Dimethyl-1H-pyrazol-4-yl)propoxy)-4-fluorobenzoic acid
4-((E)-(5-(2-(2-((S)-2-((S)-1-(L-threonyl-L-lysyl)pyrrolidine-2-carboxamido)-5-guanidinopentanamido)acetamido)-2-carboxyethyl)-2-hydroxyphenyl)diazenyl)phenyl (2-(trimethylammonio)ethyl) phosphate
Adalimumab
Arimoclomol citrate
Aviptadil
Bevacizumab
Bosentan
Caprine hyperimmune serum against HIV lysate
Carboxy pyrrolidine hexanoyl pyrrolidine carboxylate
Chimeric fibril-reactive IgG1k monoclonal antibody 11-1F4
Cyclo {{(E,Z)-(2S,3R,4R)-3-hydroxy-4-methyl-2-(methylamino)nona-6,8-dienoyl}-L-2-aminobutyryl-N-methyl-glycyl-N-methyl-L-leucyl-L-valyl-N-methyl-L-leucyl-L-alanyl-Dalanyl-N-methyl-L-leucyl-N-methyl-L-leucyl-N-methyl-L-valyl}
DNA plasmid encoding a recombinant fusion protein consisting of the extracellular domain of human TNFalpha p55 receptor linked to the human IgG1 Fc domain
Daratumumab
Doxycycline hyclate
E. Coli heat-shock protein 70 with bovine retinal S-antigen
Eculizumab
Eprodisate
Etamsylate
Fluocinolone acetonide (prolonged-release intravitreal implant)
Gevokizumab
HLA-B27 derived peptide (amino acid 125-138)
Hexasodium phytate
Human Staphylococcus aureus polyclonal immunoglobulin and human Staphylococcus epidermidis polyclonal immunoglobulin
Human engineered monoclonal antibody specific for transforming growth factor ß1
Human normal immunoglobulin
Human plasminogen
Humanised Fc-engineered monoclonal antibody against CD19
Humanised IgG1 kappa antibody against serum amyloid A and AL amyloid
Iodine (123I) Serum Amyloid P
Ixazomib
L-Pyr-L-Glu-L-Gln-L-Leu-L-Glu-L-Arg-L-Ala-L-Leu-L-Asn-L-Ser-L-Ser
Lenabasum
Lipopolysaccharide of Ochrobactrum intermedium
Melatonin
N-(3,4-dihydroxyphenyl)-3,4-dihydroxybenzamide
Nintedanib
Nitric oxide
Nitroglycerin
Octenidine dihydrochloride
Pagibaximab
Paquinimod
Patisiran
Peptide 144 TGF-beta1-inhibitor (TSLDASIIWAMMQN)
Phosphorothioate oligonucleotide targeted to transthyretin
Pomalidomide
Raloxifene hydrochloride
Recombinant human monoclonal antibody against activin receptor type IIB
Recombinant human monoclonal antibody to human Interleukin (IL)-17A of the IgG1/k class
Recombinant monoclonal antibody to human serum amyloid P component
Revusiran
Riociguat
Siponimod
Sirolimus
Sodium thiosulfate
Tafamidis
Terguride
Thalidomide
Tocilizumab
Treprostinil diethanolamine (oral use)
Triamcinolone
Type I native bovine skin collagen
Vemurafenib
Voclosporin
autologous adipose tissue-derived stromal vascular fraction cells
florbetaben (18F)
romilkimab
synthetic double-stranded siRNA oligonucleotide targeted against transthyretin mRNA, with six phosphorothioate linkages in the backbone, and nine 2'-fluoro and thirty-five 2'-O-methyl nucleoside residues in the sequence, which is covalently linked via a phosphodiester group to a ligand containing three N-acetylgalactosamine residues
ziritaxestat