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Wyszukaj lek sierocy
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(1E,6E)-1,7-bis(3,4-dimethoxyphenyl)-4-cyclobutylmethyl-1,6-heptadiene-3,5-dione (2'R,3'S)-2'-hydroxy-N-carboxy-3'-amino-5'-methyl-hexanoic,N-tert-butyl ester, 13 ester 5B-20-epoxy-1B,2a,4a,7B,9a,10a,13a-heptahydroxy-4,10-diacetate-2-benzoate-(1"S)-7,9-acrolein acetal-11(15-1)-abeotaxane (R)-troloxamide quinone 2'-O-(2-methoxyethyl) antisense oligonucleotide targeting microtubule-associated protein tau pre-mRNA 2'-O-(2-methoxyethyl) modified oligonucleotide targeted to huntingtin RNA 2'-O-methyl phosphorothioate RNA oligonucleotide, 5'-m5CUGm5CUGm5CUGm5CUGm5CUGm5CUGm5CUG-3' 2,3,4,5 tetrahydro-2,8-dimethyl-5-[2-(6-methyl-3-pyridinyl)ethyl]-1H-pyrido[4,3-b]indole dihydrochloride 2-(3,7-Dimethyl-octa-2, 6-dienyl)-6-ethylamino-3-hydroxy-5-pentyl-[1,4]benzoquinone 3,3',5-triiodothyroacetic acid (TRIAC) 3,5-diiodothyropropionic acid (DITPA) 4-hydroxy-6-{2-[4-(trifluoromethyl)phenyl]ethyl}pyridazin-3(2H)-one 5,7-dichloro-2-dimethylaminomethyl-8-hydroxyquinoline hydrochloride 5,7-dichloro-2-methylaminomethyl-8-hydroxyquinolone hydrochloride 5-bromo-N-(prop-2-yn-1-yl)-2-(1H-1,2,4-triazol-1-yl) pyrimidine-4,6-diamine 9-cis, 12-cis-11,11-D2-linoleic acid ethyl ester Lactobacillus plantarum AASSGVSTPGSAGHDIITEQPRS (P42 peptide) Acetylleucine Adeno-associated viral vector serotype 5 encoding a microRNA targeted to human huntingtin gene Adeno-associated viral vector serotype 9 containing the human CLN1 gene Adeno-associated viral vector serotype rh10 containing the human cholesterol 24-hydroxylase gene Adeno-associated virus serotype 9 containing the human ASPA gene Allogeneic motor neuron progenitor cells derived from human embryonic stem cells Alpha-tocotrienol quinone Ambroxol hydrochloride Arimoclomol Arimoclomol citrate Autologous adipose derived mesenchymal stromal cells Autologous bone marrow-derived mesenchymal stromal cells secreting neurotrophic factors Autologous haematopoietic stem cells transduced with lentiviral vector Lenti-D encoding the human ABCD1 cDNA Autologous olfactory neural progenitors Caprine hyperimmune serum against HIV lysate Carbenoxolone Ceftriaxone Chenodeoxycholic acid Cysteamine bitartrate DNA plasmid vector (pCK-HGFX7) expressing human hepatocyte growth factor Davunetide Deferiprone Deutetrabenazine Dexamethasone sodium phosphate encapsulated in human erythrocytes Dexpramipexole Dimethyl fumarate Edaravone Enoxacin Ethyl eicosopentaenoate Filgrastim Fosmetpantotenate Gemfibrozil H-Leu-Pro-Pro-Leu-Pro-Tyr-Pro-OH Human culture expanded autologous mesenchymal stromal cells Humanised IgG4 monoclonal antibody against extracellular tau Hydrocinnamate-[Orn-Pro-dCha-Trp-Arg]acetate Hydroxy-Propyl-Beta-Cyclodextrin Hydroxypioglitazone Ibudilast Interferon gamma Interferon gamma 1b Levosimendan Lithium citrate tetrahydrate (in reverse-micelle formulation) Masitinib mesilate Methylthioninium Miglustat N-(3-(4-(3-(diisobutylamino)propyl)piperazin -1-yl)propyl)-1H-benzo[d]imidazol-2-amine disulphate N-(6-(2-aminophenylamino)-6-oxohexyl)-4-methylbenzamide Olesoxime Oligopeptide containing 6 amino acids (H-Phe-Ser-Arg-Tyr-Ala-Arg-OH) Omaveloxolone Pentamer formyl thiophene acetic acid Phosphodiesterase 10 (PDE10) Inhibitor Pioglitazone Porcine fetal neural gabaergic cells and/or precursors aseptically prepared and coated with anti-Mhc-1 Ab for intracerebral implantation Porcine fetal neural gabaergic cells and/or precursors aseptically prepared for intracerebral implantation for Huntington's disease Pridopidine Recombinant adeno-associated viral vector serotype 5 carrying the gene for the human frataxin protein Recombinant human antibody directed against misfolded human superoxide dismutase 1 Recombinant human cerebral dopamine neurotrophic factor (CDNF) Recombinant human galactocerebrosidase Recombinant human heat shock protein 70 Recombinant human tripeptidyl-peptidase 1 Recombinant human vascular endothelial growth factor Recombinant humanised monoclonal antibody to human Nogo-A protein of the IgG1/kappa class Recombinant self-complementary adeno-associated viral vector serotype 9 containing the human CLN3 gene Reldesemtiv Riluzole S-acetyl-(S)-4'-phosphopantetheine, calcium salt S[+] apomorphine Sarsasapogenin Selisistat Sinbaglustat Smilagenin Sodium chlorite Sodium phenylbutyrate, tauroursodeoxycholic acid Synthetic ribonucleic acid oligonucleotide directed against superoxide dismutase 1 (SOD-1) messenger ribonucleic acid Talampanel Tauroursodeoxycholic acid (TUDCA) Temsirolimus Tilavonemab Tirasemtiv Tolfenamic acid Trans-resveratrol Trehalose Tyr-Gly-Arg-Lys-Lys-Arg-Arg-Gln-Arg-Arg-Gly-Gly-Asp-Leu-Leu-Pro-Arg-Gly-Ser Ursodeoxycholic acid Xaliproden hydrochloride [5,10,15,20-tetrakis(4-carboxyphenyl)-21H,23H-porphine]manganese(III) chloride adeno-associated viral vector serotype 9 encoding miRNA against human superoxide dismutase 1 idebenone phenol, 4-[2-(aminomethyl)-4-thiazolyl]-2,6-bis(1,1-dimethylethyl) monohydrochloride recombinant self-complementary adeno-associated viral vector serotype 9 (AAV9) containing the human CLN3 gene recombinant self-complementary adeno-associated viral vector serotype 9 containing the human CLN6 gene tideglusib
