Pesquisar um medicamento órfão
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9 Resultado(s)
Medicamento(s)
- 5'-Fosfato piridoxal
- Droxidopa
- L-threo-3,4-dihydroxyphenylserine
- Sapropterina
- Tetrahidrobiopterina
- particles comprised of methacrylic acid based co-polymer, cross-linked with a bi-functional cross-linker, purified to bind L-phenylalanine and L-phenylalanine containing peptides
- recombinant adeno-associated viral vector serotype 2 carrying the gene for the human aromatic L-amino acid decarboxylase protein