Pesquisar um medicamento órfão
Outras opções de pesquisa
169 Resultado(s)
Medicamento(s)
- 11-(2-pirrolidina-1-yl-etoxi)-14,19-dioxa-5,7,26-triaza-tetraciclo[19.3.1.1(2,6).1(8,12)] heptacosa-1(25),2(26),3,5,8,10,12(27),16,21,23-deceno
- A highly purified formulation of Staphylococcus aureus protein A
- Acetato de desmopressina
- Adeno-Associated Viral Vector (FLT180a) carrying the Factor IX gene
- Adeno-associated viral vector serotype 5 containing a B-domain deleted variant of human coagulation factor VIII gene
- Adeno-associated viral vector serotype 8 containing a functional copy of the codon-optimised F8 cDNA encoding the B-domain deleted human coagulation factor VIII
- Adeno-associated viral vector serotype 8 containing the human factor-VII gene
- Anagrelide
- Anti-von Willebrand Aptamer
- Anticorpo monoclonal IgG4 modificado humanizado com estrutura biespecífica dirigido contra os fatores IX, IXa, X e Xa
- Antithrombin alfa
- Antitrombina III (Humana)
- Autologous CD34+ cells transduced with the W1.6_hWASP_WPRE lentiviral vector
- Autologous dendritic cells incubated ex vivo with zebularine and factor VIII
- Avatrombopag
- Complexo anti-inibidores da coagulação
- Complexo factor anti-hemofílico/facto de Von Willebrand (humano)
- Células autólogas CD34+ transfectadas com um vector lentiviral que contém o gene humano da proteína do síndrome de Wiskott-Aldrich
- Defibrotide
- Efgartigimod alfa
- Eltrombopag olamina
- Eptacog alfa (activated)
- Factor VIII Porcino Recombinante (dmínio B eliminado)
- Factor VIII mimetic bispecific antibody
- Factor VIII recombinante humano peguilado de sequência modificada com eliminação do domínio B
- Factor VIIa recombinante humano de sequência modificada
- Factor XIII A-Subunit (recombinant)
- Factor XIII Concentrate (Human)
- Factor de von Willebrand humano recombinante
- Fator VIIa da coagulação recombinante modificado com três repetições terminais derivadas da cadeia beta da gonadotrofina coriónica humana
- Fedratinib
- Fibrinogénio humano
- Fidanacogene elaparvovec
- Fostamatinib disodium
- Human coagulation factor IX (antihemophilic B factor)
- Human coagulation factor VIII (antihemophilic A factor)
- Human coagulation factor X (Stuart factor)
- Human coagulation factor XI
- Human monoclonal IgG1 antibody against tissue factor pathway inhibitor
- Human monoclonal IgG2 antibody against tissue factor pathway inhibitor
- Human plasma derived coagulation protein-Factor XI
- Humanised IgG4 monoclonal antibody against total complement component 1, subcomponent
- Humanised monoclonal IgG4 antibody against tissue factor pathway inhibitor
- Imunoglobulina humana anti-Rho (D)
- Imunoglobulina humana anti-antigénio-1a plaquetário
- Imunoglobulina normal humana
- Lentiviral vector containing the human Wiskott Aldrich syndrome protein gene
- Lentiviral vector encoding human coagulation factor IX
- Lepirudina
- Long acting recombinantFactor VIIa-CTP3
- Marzeptacog alfa (activated)
- Moroctocog alpha
- N-(cianometil)-4-(2-{[4-(morfolina-4-il)fenil]amino}pirimidina-4-il)cloridrato de benzamida
- N-acetyl-D-mannosamine monohydrate
- N-terc-butil-3-[(5-metil-2-{[4-(2-pirrolidina-1-iletoxi)fenil]amino}pirimidin-4-il)amino] benzenosulfonamida diidrocloreto de monoidrato
- Nanobody (nanocorpo) específico para o domínio A1 do factor von Willebrand humano
- Nonacog alpha
- Nonacog beta pegol
- Nonacog gamma
- Octocog alfa (liposomal)
- Octocog alpha
- Oligonucleótido sintético siRNA de cadeia dupla dirigido contra o mRNA da antitrombina e com ligação covalente a um ligante contendo três resíduos de N-acetilgalactosamina
- Pegylated recombinant factor VIIa
- Plitidepsina
- Pomalidomida
- Proteína C humana
- Proteína de fusão recombinante, ligando o factor IX de coagulação humana à albumina humana
- Proteína de fusão recombinante, ligando o factor VIIa de coagulação humana à albumina humana
- Proteína recombinante de fusão que consiste no factor VIII da coagulação humana ligado ao domínio Fc da IgG1 humana
- Recombinant adeno-associated viral vector containing a codon-optimized Padua derivative of human coagulation factor IX cDNA
- Recombinant adeno-associated viral vector serotype 6 encoding the B-domain-deleted human factor VIII
- Recombinant fusion protein consisting of human coagulation factor IX attached to the Fc domain of human IgG1
- Recombinant human ADAMTS-13
- Recombinant human factor XIII (composed of two A subunits)
- Recombinant human soluble Fc-gamma receptor II b
- Recombinant megakaryopoeisis-stimulating protein
- Rilzabrutinib
- Rituximab
- Rozanolixizumab
- Ruxolitinib
- Vatreptacog alfa (activated)
- Vector viral adeno-associado contendo o gene do factor IX humano
- Von Willebrand human factor
- adeno associated virus with modified transthyretin and sequence encoding factor IX variant gene
- anti-(integrin beta-3) human monoclonal antibody
- glycoPEGylated recombinant coagulation factor VIII
- recombinant AAV vector with hu37 serotype capsid (AAVhu37) encoding human FVIII
- recombinant adeno-associated viral vector containing a bioengineered capsid and a codon-optimised expression cassette to drive the expression of the SQ form of a B-domain deleted human coagulation factor VIII
- recombinant human coagulation factor VIII Fc - von Willebrand factor - XTEN fusion protein
- recombinant human factor IX protein modified with three point mutations
- Ácido siálico
Nome(s) de comercialização
- ACLOTINE
- ADVATE
- ADYNOVI
- AFSTYLA
- AGRYLIN
- ALPHANATE
- ALPHANINE
- ALPROLIX
- ANAGRELIDE MYLAN
- ATNATIV
- ATRYN
- BENEFIX
- BETAFACT
- CABLIVI
- CEPROTIN
- CLOTTAGEN
- COAGADEX
- CORIFACT
- DESMOPRESSIN ACETATE AVENTIS BEHRING L.L.C.
- DOPTELET
- ELOCTA
- ELOCTATE
- ENDOBULINE
- ESPEROCT
- FACTANE
- FACTEUR VII LFB
- FEIBA
- FLEBOGAMMA DIF
- GAMMAGARD
- GAMMAPLEX
- HAEMOCOMPLETTAN
- HELIXATE NEXGEN
- HEMLIBRA
- HEMOLEVEN
- HUMATE -P
- HYDREA
- IBLIAS
- IDELVION
- INREBIC
- INTRAGLOBIN F
- JAKAFI
- JAKAVI
- JIVI
- KASKADIL
- KIOVIG
- KOGENATE BAYER
- KOVALTRY
- NONAFACT
- NOVOEIGHT
- NOVOSEVEN
- NOVOSEVEN RT
- NOVOTHIRTEEN
- NPLATE
- OBIZUR
- OCTAGAM
- OCTIM
- PRIVIGEN
- PROMACTA
- PROTEXEL
- REFACTO AF
- REFIXIA
- REFLUDAN
- REFLUDEN
- REVOLADE
- RIASTAP
- RIXUBIS
- SANDOGLOBULINE
- TAVALISSE
- TEGELINE
- THROMBATE III
- TRETTEN
- VEYVONDI
- VONCENTO
- VONVENDI
- WILFACTIN
- WILSTART
- WINRHO SD
- XAGRID