Search for an orphan drug
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- INN (International Nonproprietary Name) : Sirolimus
- Code name : -
- Chemical name or description : -
- Type of product : Ingredient/substance
- Type of production : Synthetic / extractive chemistry
- Orphan designation :
Orphan designation - Europe
- Diseases list
- Complication in hemodialysis
- Detailed information
Orphan designation - Europe
- Diseases list
- Tuberous sclerosis complex
- Detailed information
Orphan designation - Europe
- Diseases list
- Beta-thalassemia major
- Beta-thalassemia intermedia
- Detailed information
Orphan designation - Europe
- Diseases list
- Lymphangioleiomyomatosis
- Detailed information
Orphan designation - Europe
- Diseases list
- Tuberous sclerosis complex
- Detailed information
Orphan designation - Europe
- Diseases list
- Pachyonychia congenita
- Detailed information
Orphan designation - Europe
- Diseases list
- Tuberous sclerosis complex
- Detailed information
Orphan designation - Europe
- Diseases list
- Sickle cell anemia
- Detailed information
Orphan designation - Europe
- Diseases list
- Perivascular epithelioid cell neoplasm
- Detailed information
Orphan designation - Europe
- Diseases list
- Bronchiolitis obliterans with obstructive pulmonary disease
- Detailed information
Orphan designation - Europe
- Diseases list
- Rare lymphatic malformation
- Detailed information
Orphan designation withdrawn/expired - Europe
- Diseases list
- Intermediate uveitis
- Idiopathic panuveitis
- Non-infectious anterior uveitis
- Systemic diseases with panuveitis
- Systemic diseases with anterior uveitis
- Systemic diseases with posterior uveitis
- Detailed information
Orphan designation - USA
- Diseases list
- Lymphangioleiomyomatosis
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
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