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Carglumic acid

UCEDANE   CARBAGLU   
  • INN (International Nonproprietary Name) : Carglumic acid
  • Code name : -
  • Chemical name or description : N-carbamyl-L-glutamic acid
  • Type of product : Ingredient/substance
  • Type of production : Synthetic / extractive chemistry
  • Orphan designation : EuropeUSA
    • Orphan designation  - Europe

    • Diseases list
      • Methylmalonic acidemia with homocystinuria
      • Methylmalonic acidemia without homocystinuria
    • Detailed information
    • Orphan designation withdrawn  - Europe

    • Diseases list
      • Hyperammonemia due to N-acetylglutamate synthase deficiency
    • Detailed information
    • Orphan designation  - USA

    • Diseases list
      • Propionic acidemia
      • Isovaleric acidemia
      • Methylmalonic acidemia with homocystinuria
      • Methylmalonic acidemia without homocystinuria
    • Detailed information

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