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Luspatercept
REBLOZYL- INN (International Nonproprietary Name) : luspatercept
- Code name : ACE-536
- Chemical name or description : Recombinant fusion protein consisting of a modified form of the extracellular domain of human activin receptor IIB linked to the human IgG1 Fc domain
- Type of product : Ingredient/substance
- Type of production : Biotechnology
- Orphan designation :
Orphan designation - Europe
- Diseases list
- Beta-thalassemia major
- Beta-thalassemia intermedia
- Detailed information
Orphan designation - Europe
- Diseases list
- Myelodysplastic syndrome
- Detailed information
Orphan designation - Europe
- Diseases list
- Primary myelofibrosis
- Detailed information
Orphan designation - USA
- Diseases list
- Beta-thalassemia
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
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