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Autologous bone marrow CD34+ cells transduced ex vivo with a self activating HIV-1 -based lentiviral vector, EFS-ADA

  • INN (International Nonproprietary Name) : -
  • Code name : -
  • Chemical name or description : -
  • Type of product : Ingredient/substance
  • Type of production : Biotechnology
  • Orphan designation : USA
    • Orphan designation  - USA

    • Diseases list
      • Severe combined immunodeficiency due to adenosine deaminase deficiency
    • Detailed information

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