Search for an orphan drug
Other search option(s)
YARGESA
MiglustatMarketing authorisation without orphan designation - Europe
- Diseases list
- Gaucher disease type 1
- Detailed information
Marketing authorisation without orphan designation - Europe
- Diseases list
- Niemann-Pick disease type C
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
The documents contained in this web site are presented for information purposes only. The material is in no way intended to replace professional medical care by a qualified specialist and should not be used as a basis for diagnosis or treatment.