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- INN (International Nonproprietary Name) : Miglustat
- Code name : -
- Chemical name or description : 1,5-(Butylimino)-1,5-dideoxy, D-glucitol
- Type of product : Ingredient/substance
- Type of production : Synthetic / extractive chemistry
- Orphan designation :
Orphan designation - Europe
- Diseases list
- Neuronal ceroid lipofuscinosis
- Detailed information
Orphan designation withdrawn/expired - Europe
- Diseases list
- Gaucher disease
- Detailed information
Orphan designation withdrawn/expired - Europe
- Diseases list
- Niemann-Pick disease type C
- Detailed information
Orphan designation withdrawn/expired - Europe
- Diseases list
- Glycogen storage disease due to acid maltase deficiency
- Detailed information
Orphan designation - USA
- Diseases list
- Gaucher disease
- Detailed information
Additional information
Research on this medical product
Appraisal/reimbursement
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