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27 Ergebnis(se)
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Nationale klinische Studie(n)

Comunidad Valenciana
VALENCIA
A Phase 2b Efficacy and Safety Study of PTC124 in Subjects With Nonsense-Mutation-Mediated Duchenne Muscular Dystrophy and Becker Muscular Dystrophy - ES (completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
A Phase II, Double Blind, Exploratory, Parallel-group, Placebo controlled Clinical Study to Assess Two Dosing Regimens of GSK2402968 for Efficacy, Safety, Tolerability and Pharmacokinetics in Ambulant Subjects With Duchenne Muscular Dystrophy - ES - (Participation is dependent on local ethics committee approval) (completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
DELOS: A Phase III Double-Blind, Randomised, Placebo-Controlled Study of the Efficacy, Safety and Tolerability of Idebenone in 10-18 Year Old Patients with Duchenne Muscular Dystrophy - ES (completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
A Randomized, Double-Blind, Placebo-Controlled, Phase 3 Trial of Tadalafil for Duchenne Muscular Dystrophy - ES (Completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
LIME Study: A European, Randomised, Double-blind, Active Comparator Controlled, Cross-over, Efficacy and Safety Study of a New 10% Ready To-use Liquid Human Intravenous Immunoglobulin (I10E) Versus Kiovig® in Patients With Multifocal Motor Neuropathy (Phase III) - ES (Completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
A Phase 3 Extension Study of Ataluren (PTC124) in Patients with Nonsense Mutation Dystrophinopathy - ES (Completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
PRISM 2: International, multicentre, efficacy and safety study of I10E in the maintenance treatment of patients with Chronic Inflammatory Demyelinating Polyradiculoneuropathy: Extension of PRISM study I10E-1302 (Phase III) - ES (Completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
International, multi-center, randomized, double-blind, placebo-controlled phase III study assessing in parallel groups the efficacy and safety of 2 doses of PXT3003 in patients with Charcot-Marie-Tooth Disease type 1A treated 15 months - ES (completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
PRISM: An international, multicentre, efficacy and safety study of I10E in initial and maintenance treatment of patients with Chronic Inflammatory Demyelinating Polyradiculoneuropathy (Phase III) - ES (completado)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
A Phase III Study to Evaluate the Efficacy, Safety, and Tolerability of Immune Globulin Infusion 10% (Human) with Recombinant Human Hyaluronidase (HYQVIA/HyQvia) and Immune Globulin Infusion (Human), 10% (GAMMAGARD LIQUID/KIOVIG) for the Treatment of Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP) - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
PLEO-CMT-FU: International, multi-center, double blind 9-month FOLLOW-UP extension study assessing the long term safety and tolerability of PXT3003 in patients with Charcot-Marie-Tooth Disease type 1A - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA


Long-Term Tolerability and Safety of Immune Globulin Infusion 10% (Human) with Recombinant Human Hyaluronidase (HYQVIA/HyQvia) for the Treatment of Chronic Inflammatory Demyelinating Polyradiculoneuropathy (CIDP) (Phase III) - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
A Randomized, Double Blind, Placebo-Controlled, Study to Assess the Efficacy, Safety, and Tolerability of BMS-986089 in Ambulatory Boys with Duchenne Muscular Dystrophy (Phase III) - ES (completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA


COMET: A Phase 3 Randomized, Multicenter, Multinational, Double-blinded Study Comparing the Efficacy and Safety of Repeated Biweekly Infusions of NeoGAA (GZ402666) and Alglucosidase Alfa in Treatmentnaïve Patients with Late-onset Pompe Disease - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA

A Double-Blind, Placebo-Controlled, Multicenter Study With an Open-Label Extension to Evaluate the Efficacy and Safety of SRP-4045 and SRP-4053 in Patients With Duchenne Muscular Dystrophy (Phase III) - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA

Long-term, open-label extension study for patients with Duchenne muscular dystrophy enrolled in clinical trials evaluating casimersen or golodirsen - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA

SIDEROS-E: A phase III open-label extension study to assess the long-term safety and efficacy of idebenone in patients with Duchenne muscular dystrophy (DMD) who completed the SIDEROS study - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
REFALS-ES: Effects of oral Levosimendan (ODM-109) on respiratory function in patients with ALS: open label extension for patients completing study 3119002 (Phase III) - ES (completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
VIVACITY-MG: A Phase 2, Multicenter, Randomized, Double-Blind, Placebo-Controlled Study to Evaluate the Safety, Tolerability, Efficacy, Pharmacokinetics and Pharmacodynamics of M281 Administered to Adults with Generalized Myasthenia Gravis - ES (completed)
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
HELIOS-A: A Phase 3 Global, Randomized, Open-label Study to Evaluate the Efficacy and Safety of ALN-TTRSC02 in Patients with Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis) - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA

A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Safety and Efficacy of Ravulizumab in Complement-Inhibitor-Naïve Adult Patients With Generalized Myasthenia Gravis - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA

A Randomized, Multicenter, Double-Blind, Placebo-Controlled, Phase III Clinical Study to Evaluate the Efficacy and Safety of Intrathecally Administered RO7234292 (RG6042) in Patients With Manifest Huntington's Disease - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA

Randomised, double blind, placebo controlled, multicentre study to evaluate the efficacy and safety of givinostat in ambulant patients with Duchenne Muscular Dystrophy (Phase III) - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA

A Phase 3, External Placebo-Controlled, Open-Label, Multicenter Study to Evaluate the Efficacy and Safety of Ravulizumab in Adult Patients With Neuromyelitis Optica Spectrum Disorder (NMOSD) - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA

A Phase 2, Randomized, Placebo-Controlled Study to Evaluate Safety, Tolerability, and Efficacy of TAK-079 in Patients With Generalized Myasthenia Gravis - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA
An Open-label Extension Study of MOM-M281-004 to Evaluate the Safety, Tolerability, and Efficacy of M281 Administered to Patients with Generalized Myasthenia Gravis (Phase II) - ES
Hospital Universitario y Politécnico La Fe
Servicio de Neurología

Comunidad Valenciana
VALENCIA