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National clinical trial(s)
ITALY
LOMBARDIA
MILANO
INTEGRATION CORE: integration site analysis in a clinical trial of lentiviral vector based hematopoietic stem cell gene therapy for metachromatic leukodystrophy
IRCCS Ospedale San Raffaele
Centro di Genomica, Bioinformatica e Biostatistica - Unità di Genetica Umana e Molecolare
ITALY
LOMBARDIA
MILANO
A Phase I/II Clinical Trial of Hematopoietic Stem Cell Gene Therapy for the Treatment of Metachromatic Leukodystrophy
Istituto San Raffaele Telethon per la Terapia Genica - TIGET
Unità di Ricerca Clinica
ITALY
LOMBARDIA
MILANO
A Single Arm, Open Label, Clinical Study of Cryopreserved Autologous CD34+ Cells Transduced With Lentiviral Vector Containing Human ARSA cDNA (GSK2696274), for the Treatment of Early Onset Metachromatic Leukodystrophy (MLD)
Istituto San Raffaele Telethon per la Terapia Genica - TIGET
Unità di Ricerca Clinica
BELGIUM
ANTWERPEN
EDEGEM (ANTWERPEN)
Embolden: A Global, Multicenter, Open-label, Matched Historical Control Study of Intrathecal SHP611 in Subjects With Late Infantile Metachromatic Leukodystrophy - BE
Antwerp University Hospital - UZA
Department of pediatric metabolic diseases (Metabole stoornissen kinderen/Metabolic Disorders in Children)
CANADA
Québec
ADDRESS: NOT PROVIDED - CA
EMBOLDEN: A Glob-al, Multicenter, Open-label, Matched Historical Control Study of Intrathecal SHP611 in Subjects With Late Infantile Metachromatic Leukodystrophy-CA
Institution: Information not provided - CA
GERMANY
Baden-Württemberg
TÜBINGEN
Embolden: A Global, Multicenter, Open-label, Matched Historical Control Study of Intrathecal SHP611 in Subjects With Late Infantile Metachromatic Leukodystrophy -DE-
Universitätsklinikum Tübingen
GERMANY
Hamburg
HAMBURG
Embolden: A Global, Multicenter, Open-label, Matched Historical Control Study of Intrathecal SHP611 in Subjects With Late Infantile Metachromatic Leukodystrophy -DE-
UKE - Universitätsklinikum Hamburg-Eppendorf
Klinik und Poliklinik für Kinder- und Jugendmedizin
SPAIN
Cataluña
BARCELONA
A Global, Multicenter, Open-label, Matched Historical Control Study of Intrathecal SHP611 in Subjects with Late Infantile Metachromatic Leukodystrophy -ES
Hospital Universitari Vall d'Hebron
Servicio de Neurología Pediátrica
Multinational clinical trial(s)
IRELAND
County Dublin
ADDRESS: NOT PROVIDED - IE