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Recruiting trial = Recruiting trial
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National clinical trial(s)

ITALY

LOMBARDIA
MILANO

Ongoing trial
Funded by an IRDiRC memberINTEGRATION CORE: integration site analysis in a clinical trial of lentiviral vector based hematopoietic stem cell gene therapy for metachromatic leukodystrophy
IRCCS Ospedale San Raffaele
Centro di Genomica, Bioinformatica e Biostatistica - Unità di Genetica Umana e Molecolare

ITALY

LOMBARDIA
MILANO

Recruiting trial
Ongoing trial
Funded by an IRDiRC memberA Phase I/II Clinical Trial of Hematopoietic Stem Cell Gene Therapy for the Treatment of Metachromatic Leukodystrophy
Istituto San Raffaele Telethon per la Terapia Genica - TIGET
Unità di Ricerca Clinica

BELGIUM

ANTWERPEN
EDEGEM (ANTWERPEN)

Recruiting trial
Ongoing trial
Funded by an IRDiRC memberEmbolden: A Global, Multicenter, Open-label, Matched Historical Control Study of Intrathecal SHP611 in Subjects With Late Infantile Metachromatic Leukodystrophy - BE
University Hospital Antwerp - UZA
Department of pediatric metabolic diseases (Metabole stoornissen kinderen/Metabolic Disorders in Children)

GERMANY

Hamburg
HAMBURG