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Recruiting trial = Recruiting trial
; Ongoing trial = Ongoing trial
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National clinical trial(s)

GERMANY

Baden-Württemberg
FREIBURG

Ongoing trial
Can treatment with human growth hormone increase strength in spinal muscular atrophy type II and III (phase II study)?
Zentrum für Kinder- und Jugendmedizin Freiburg
Klinik für Neuropädiatrie und Muskelerkrankungen

GERMANY

Baden-Württemberg
FREIBURG

ITALY

LOMBARDIA
MILANO

Recruiting trial
Ongoing trial
Long Term Safety Study of Amifampridine Phosphate in Ambulatory Patients With Spinal Muscular Atrophy (SMA) Type 3
Fondazione IRCCS Istituto Neurologico "Carlo Besta"
U.O. Neurologia IV - Malattie Neuromuscolari e Neuroimmunologia

SPAIN

Cataluña
ESPLUGUES DE LLOBREGAT

BELGIUM

ARRONDISSEMENT BRUSSELS-CAPITAL
BRUSSELS

BELGIUM

LIEGE
LIEGE

Recruiting trial
Ongoing trial
Funded by an IRDiRC memberRAINBOWFISH: An Open-Label Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy - BE
Centre Hospitalier Régional de la Citadelle
Centre de Référence des Maladies Neuromusculaires (CRMN)

FRANCE

ILE-DE-FRANCE
PARIS

FRANCE

ILE-DE-FRANCE
GARCHES

Ongoing trial
Long-Term Effect of LIAM (Lung Insufflation Assist Maneuver) on Respiratory Performance in Non-invasive Ventilated Patients Suffering From Neuromuscular Disease - FR
CHU Paris IdF Ouest - Hôpital Raymond Poincaré
Centre d'Investigation Clinique et Technologique 805 - CIC-IT de Garches

FRANCE

ILE-DE-FRANCE
GARCHES

Ongoing trial
Establishment of a Non-invasive and Indirect Measure of Volitional Pimax (PI MAX STIM) - FR
CHU Paris IdF Ouest - Hôpital Raymond Poincaré
Service de Physiologie-Explorations Fonctionnelles

Multinational clinical trial(s)