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National clinical trial(s)

AUSTRIA

WIEN
WIEN

Recruiting trial
Ongoing trial
Funded by an IRDiRC memberHCQ4Surfdefect: Hydroxychloroquine (HCQ) in pediatric ILD (interstitial lung disease) - AT
Allgemeines Krankenhaus der Stadt Wien
Klinische Abteilung für Pädiatrische Pulmologie, Allergologie und Endokrinologie

FRANCE

AUVERGNE-RHONE-ALPES
GRENOBLE

GERMANY

Baden-Württemberg
TÜBINGEN

Recruiting trial
Ongoing trial
TOFFIFE: Tocilizumab for the Treatment of Familial Mediterranean Fever - A randomized, doubleblind, phase II proof of concept study
Interdisziplinäres Rheumazentrum (INDIRA)
Zentrum für Interdisziplinäre Rheumatologie, klinische Immunologie und Autoimmunerkrankungen

ITALY

LOMBARDIA
MILANO

Ongoing trial
Funded by an IRDiRC memberTIGET-WAS - A Phase I/II Clinical Trial of Hematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich Syndrome
Istituto San Raffaele Telethon per la Terapia Genica - TIGET
Istituto San Raffaele Telethon per la Terapia Genica

SPAIN

Cataluña
ESPLUGUES DE LLOBREGAT

UNITED KINGDOM

Greater London
LONDON

UNITED STATES

Pennsylvania
PHILADELPHIA

FINLAND

Finland
HELSINKI

FRANCE

ILE-DE-FRANCE
PARIS

Recruiting trial
Ongoing trial
C-HLH : First Line Treatment of Familiar Lymphohistiocytosis by Alemtuzumab (CAMPATH®) (Phase I-II)
Hôpital Necker-Enfants Malades
Service d'Immuno-hématologie pédiatrique

GERMANY

Hessen
FRANKFURT AM MAIN

GERMANY

Hessen
FRANKFURT AM MAIN

Recruiting trial
Ongoing trial
gene therapy for X-CGD (X-CGD-Version2): A Phase I/II Gene Therapy Trial for X-CGD With a SIN Gammaretroviral Vector - DE
Klinikum der Johann Wolfgang Goethe-Universität Frankfurt
Medizinische Klinik II - Hämatologie, Onkologie, Hämostaseologie, Rheumatologie, Infektiologie

GERMANY

Hessen
FRANKFURT AM MAIN

Recruiting trial
Ongoing trial
Funded by an IRDiRC memberPhase I/II G1XCGD.01 Sudy: Phase I/II, Non Randomized, Multicenter, Open-label Study of g1xcgd (Lentiviral Vector Transduced cd34+ Cells) in Patients with X-linked Chronic Granulomatous Disease - DE
Klinikum der Johann Wolfgang Goethe-Universität Frankfurt
Medizinische Klinik II - Hämatologie, Onkologie, Hämostaseologie, Rheumatologie, Infektiologie

UNITED KINGDOM

Greater London
LONDON

Ongoing trial
Phase I/II Gene Therapy Study for X-linked Chronic Granulomatous Disease in Children
GOSH NHS Foundatin Trust
Molecular and Cellular Immunology Unit

UNITED KINGDOM

Greater London
LONDON

BELGIUM

ARRONDISSEMENT BRUSSELS-CAPITAL
BRUSSELS

FRANCE

ILE-DE-FRANCE
PARIS

Ongoing trial
SCID2 - Protocol No. 2 of gene therapy for X-linked severe combined immunodeficiency (SCID-X1) using a self retroviral vector.
Hôpital Necker-Enfants Malades
Développement normal et pathologique du système immunitaire

UNITED KINGDOM

Greater London
LONDON

Multinational clinical trial(s)

FRANCE

ILE-DE-FRANCE
EVRY

SWITZERLAND

Suisse Romande
ADDRESS: NOT PROVIDED - CH