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Recruiting trial = Recruiting trial
; Ongoing trial = Ongoing trial
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National clinical trial(s)

BELGIUM

ARRONDISSEMENT BRUSSELS-CAPITAL
BRUSSELS

ITALY

LAZIO
ROMA

Recruiting trial
Ongoing trial
A Phase 1/2 Study of ARQ 092 in Patients with Overgrowth Diseases and/or Vascular Anomalies with Genetic Alterations of the PI3K/AKT Pathway
IRCCS Ospedale Pediatrico Bambino Gesù - SEDE GIANICOLO
Ambulatorio Polispecialistico per le Malattie Rare

NETHERLANDS

Zuid-Holland
ROTTERDAM

UNITED KINGDOM

Avon
BATH

Ongoing trial
International Collaborative Infantile Spasms Study (ICISS)
Royal United Hospital Bath NHS Trust
The Childrens Centre

UNITED KINGDOM

Avon
BRISTOL

Recruiting trial
Ongoing trial
A randomized, double-blind, parallel group, placebo-controlled trial of metformin in tuberous sclerosis complex (Phase IV) - UK
Level 6, University Hospitals Bristol Education Centre
Bristol Child Neuroscience (CNS)

AUSTRIA

SALZBURG
SALZBURG

Ongoing trial
MitoFibrate CT1: Clinical study for the assessment of safety and efficacy of Bezafibrate as a drug therapy for patients with mitochondrial myopathies (phase II) - AT
Universitätsklinikum der Paracelsus Medizinischen Privatuniversität
Universitätsklinik für Kinder- und Jugendheilkunde

GERMANY

Baden-Württemberg
HEIDELBERG

Ongoing trial
SELICA II: Open, prospective, uncontrolled, multicentre study to evaluate the safety and efficacy of multiple applications of liver cell suspension into the portal vein in newborns with Urea Cycle Disorders (UCDs) (Phase II)
Zentrum für Kinder- und Jugendmedizin - Angelika-Lautenschläger-Klinik
Klinik für Kinderheilkunde I - Sektion für Neuropädiatrie und Stoffwechselmedizin

Multinational clinical trial(s)