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Essai(s) clinique(s) national(aux)

ALLEMAGNE
Berlin
ADDRESS: NOT PROVIDED - DE

AMETHIST: A multicenter, multinational, randomized, double-blind, placebo-controlled study to assess the efficacy, pharmacodynamics, pharmacokinetics, safety, and tolerability of venglustat in late-onset GM2 gangliosidosis (Tay-Sachs disease and Sandhoff disease) - DE
Institution: Information not provided - DE

AUTRICHE
WIEN
ADDRESS: NOT PROVIDED - AT

AMETHIST: A multicenter, multinational, randomized, double-blind, placebo-controlled study to assess the efficacy, pharmacodynamics, pharmacokinetics, safety, and tolerability of venglustat in late-onset GM2 gangliosidosis (Tay-Sachs disease and Sandhoff disease) - AT
Institution: Information not provided - AT
Essai(s) clinique(s) multinational(aux)

ETATS-UNIS
Massachusetts
CAMBRIDGE