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Cerca una sperimentazione clinica

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3 Risultato/i

Sperimentazione in fase di reclutamento = Sperimentazione in fase di reclutamento
; Sperimentazione in corso = Sperimentazione in corso
; Finanziato da un ente associato a IRDiRC =

Sperimentazioni cliniche nazionali

FRANCIA

AUVERGNE-RHONE-ALPES
BRON

A study of the safety, efficacy, pharmacokinetics and pharmacodynamics of recombinant human alpha glucosidase (rhGAA) treatment in patients >6 m and <36 m old with infantile onset Pompe disease (Phase II) - Terminated -
CHU de Lyon HCL - GH Est-Hôpital Femme Mère Enfant
Service d'endocrinologie et de diabétologie pédiatriques et maladies héréditaires du métabolisme

FRANCIA

AUVERGNE-RHONE-ALPES
BRON

A dose-ranging study of the safety, efficacy, pharmacokinetics and phamacodynamics of recombinant human Acid Alpha Glucosidase (rhGAA) treatment in patients <6 m old with infantile onset Pompe disease (Phase II) - Terminated -
CHU de Lyon HCL - GH Est-Hôpital Femme Mère Enfant
Service d'endocrinologie et de diabétologie pédiatriques et maladies héréditaires du métabolisme