x

Zoek een klinische studie of trial

* (*) verplicht veld

7 Resultaat/Resultaten

Aanwerving proef = Aanwerving proef
; Lopend onderzoek = Lopend onderzoek
; Gefinancierd door een IRDiRC-lid = ; Member of a ERN =

Nationale klinische studie(s)

ITALI╦

LAZIO
ROMA

Gefinancierd door een IRDiRC-lidA Phase 2b Efficacy and Safety Study of PTC124 in Subjects With Nonsense-Mutation-Mediated Duchenne Muscular Dystrophy and Becker Muscular Dystrophy - IT
IRCCS Ospedale Pediatrico Bambino Ges¨ - SEDE SAN PAOLO
UnitÓ di Malattie Neuromuscolari e Neurodegenerative - Laboratorio di Medicina Molecolare

ITALI╦

LAZIO
ROMA

Phase II, multicenter, randomized, adaptive, double-blind, placebo controlled study to assess safety and efficacy of olesoxime (TRO19622) in 3-25 year old Spinal Muscular Atrophy (SMA) patients - IT
IRCCS Ospedale Pediatrico Bambino Ges¨ - SEDE SAN PAOLO
UnitÓ di Malattie Neuromuscolari e Neurodegenerative - Laboratorio di Medicina Molecolare

ITALI╦

LAZIO
ROMA

Gefinancierd door een IRDiRC-lidAn Open-Label Study for Previously Treated Ataluren (PTC124) Patients With Nonsense Mutation Dystrophinopathy (Phase III) - IT
IRCCS Ospedale Pediatrico Bambino Ges¨ - SEDE SAN PAOLO
UnitÓ di Malattie Neuromuscolari e Neurodegenerative - Laboratorio di Medicina Molecolare

ITALI╦

LAZIO
ROMA

Aanwerving proef
Lopend onderzoek
Prospective open label trial to evaluate the maintenance of the efficacy and the long term safety of EPI-743 in children with Leigh Disease (Phase II) - IT
IRCCS Ospedale Pediatrico Bambino Ges¨ - SEDE SAN PAOLO
UnitÓ di Malattie Neuromuscolari e Neurodegenerative - Laboratorio di Medicina Molecolare

ITALI╦

LAZIO
ROMA

Aanwerving proef
Lopend onderzoek
Open Label, Long-term Safety, Tolerability, and Efficacy Study of GIVINOSTAT in All DMD Patients Who Have Been Previously Treated in One of the GIVINOSTAT Studies - IT
IRCCS Ospedale Pediatrico Bambino Ges¨ - SEDE SAN PAOLO
UnitÓ di Malattie Neuromuscolari e Neurodegenerative - Laboratorio di Medicina Molecolare

Multinationale klinische studie(s)