Orphanet: Search for an orphan drug

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Orphan designation - Europe

  • Substance: Lonafarnib
  • ATC code : -
  • EU Number: EU/3/18/2118
  • Designation date : 14/12/2018
  • Sponsor of orphan designation : EIGERBIO EUROPE LIMITED
  • Summary of Opinion


Treatment of Hutchinson-Gilford progeria.

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