Orphanet: Wyszukaj lek sierocy
Wyszukaj lek sierocy
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- (S)-(-)-3-(4-aminophenyl)-2-methoxypropanoic acid
- 2-((2-ethyl-6-(4-(2-(3-hydroxyazetidin-1-yl)-2-oxoethyl)-piperazin-1-yl)-8-methylimidazo[1,2-alpha]pyridin-3-yl)-(methyl)amino)-4-(4-fluorophenyl)-thiazole-5-carbonitrile
- 2-(2-chlorophenyl)-4-[3-(dimethylamino)phenyl]-5-methyl-1H-pyrazolo[4,3-c]pyridine-3,6(2H,5H)-dione
- 3-Pentylbenzeneacetic acid sodium salt
- 3-[4-(1H-imidazol-1-ylmethyl)phenyl]-5-(2-methylpropyl)thiophene-2-[(N-butyloxylcarbamate)-sulphonamide] sodium salt
- Acetylcysteine
- Acetylleucine
- Adalimumab
- Alglucerase
- Ambrisentan
- Antagonist of the complement 5a receptor
- Arimoclomol citrate
- Autologous CD34+ cells transduced with retroviral vector containing the human gp91 (phox) gene
- Autologous haematopoietic cells genetically modified with a lentiviral vector containing the human gp91(phox) gene
- Avacopan
- Aviptadil
- Bosentan
- Budesonide (oral use)
- Canakinumab
- Dipalmitoylphosphatidylcholine, 1-palmitoyl-2-oleoyl-sn-glycero-3-phosphoglycerol, sodium salt, synthetic surfactant protein C analogue and synthetic surfactant protein B analogue
- Drotrecogin alfa (activated)
- Eliglustat
- Etanercept
- Givinostat
- Granulocyte-macrophage colony-stimulating factor
- Gusperimus trihydrochloride
- Heparin sodium
- Humanised anti-alpha v beta 6 monoclonal antibody
- Hydroxy-Propyl-Beta-Cyclodextrin
- Imatinib mesilate
- Imiglucerase
- Interferon beta
- Interferon gamma
- Interferon gamma 1a
- Interferon gamma 1b
- L-Pyr-L-Glu-L-Gln-L-Leu-L-Glu-L-Arg-L-Ala-L-Leu-L-Asn-L-Ser-L-Ser
- Lucinactant
- Lusupultide
- Macitentan
- Meloxicam
- Mepolizumab
- Miglustat
- Molgramostim
- Nintedanib
- Nitric oxide
- Pirfenidone
- Pulmonary surfactant replacement, porcine
- Recombinant human acid sphingomyelinase
- Recombinant human heat shock protein 70
- Recombinant human monoclonal antibody against mannan-binding lectin-associated serine protease-2
- Recombinant human monoclonal antibody against transforming growth factor beta-1, 2 and 3
- Recombinant human pentraxin-2
- Rituximab
- Sinapultide, dipalmitoylphosphatidylcholine, palmitoyloleoylphosphatidylglycerol and palmitic acid
- Sirolimus
- Sodium cromoglicate
- Surface active extract of saline lavage of bovine lungs
- T-Cell Depleted Stem Cell Enriched Cellular Product From Peripheal Blood Stem Cells
- Tanzisertib
- Tilorone
- Tipelukast
- Tocilizumab
- Tralokinumab
- Ursodeoxycholic acid
- adeno-associated viral vector serotype 9 containing the human glucocerebrosidase gene
- imlifidase