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Recruiting trial = Recruiting trial
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National clinical trial(s)

UNITED KINGDOM

Greater London
LONDON

Recruiting trial
Ongoing trial
A Phase 1/2 Study of the Safety and Efficacy of a Single Dose of Autologous CRISPR-Cas9 Modified CD34+ Human Hematopoietic Stem and Progenitor Cells (hHSPCs) in Subjects With Transfusion-Dependent beta-Thalassemia-GB
Joint UCLH/UCL Biomedical Research and Development (R&D) Unit
University College London (UCL) and University College London Hospitals NHS Trust (UCLH)

ITALY

EMILIA ROMAGNA
FERRARA

Ongoing trial
An Open-Label Extension Study to Evaluate the Long-Term Effects of ACE-536 in Patients With beta-Thalassemia Previously Enrolled in Study A536-04
A.O.U. di Ferrara - Nuovo Ospedale S.Anna - Sede di Cona
Day Hospital della Talassemia e delle Emoglobinopatie

Multinational clinical trial(s)