Essai en cours de recrutement = ; Essai en cours = ; Essai terminé = ; Financé par un membre IRDiRC = ; Membre d'un ERN =

Essai(s) clinique(s) national(aux)

ITALIE

LOMBARDIA
MILANO

INTEGRATION CORE: integration site analysis in a clinical trial of lentiviral vector based hematopoietic stem cell gene therapy for metachromatic leukodystrophy

IRCCS Ospedale San Raffaele

Centro di Genomica, Bioinformatica e Biostatistica - Unità di Genetica Umana e Molecolare

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ITALIE

LOMBARDIA
MILANO

A Phase I/II Clinical Trial of Hematopoietic Stem Cell Gene Therapy for the Treatment of Metachromatic Leukodystrophy

Istituto San Raffaele Telethon per la Terapia Genica - TIGET

Unità di Ricerca Clinica

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ITALIE

LOMBARDIA
MILANO

A Single Arm, Open Label, Clinical Study of Cryopreserved Autologous CD34+ Cells Transduced With Lentiviral Vector Containing Human ARSA cDNA (GSK2696274), for the Treatment of Early Onset Metachromatic Leukodystrophy (MLD)

Istituto San Raffaele Telethon per la Terapia Genica - TIGET

Unità di Ricerca Clinica

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